PRODUCTION OF HUMAN GLUCOCEREBROSIDASE IN MICE AFTER RETROVIRAL GENE-TRANSFER INTO MULTIPOTENTIAL HEMATOPOIETIC PROGENITOR CELLS

被引:45
作者
CORRELL, PH [1 ]
FINK, JK [1 ]
BRADY, RO [1 ]
PERRY, LK [1 ]
KARLSSON, S [1 ]
机构
[1] NINCDS,DEV & METAB NEUROL BRANCH,MOLEC & MED GENET SECT,BLDG 10,ROOM 3D04,BETHESDA,MD 20892
关键词
D O I
10.1073/pnas.86.22.8912
中图分类号
O [数理科学和化学]; P [天文学、地球科学]; Q [生物科学]; N [自然科学总论];
学科分类号
07 ; 0710 ; 09 ;
摘要
引用
收藏
页码:8912 / 8916
页数:5
相关论文
共 38 条
[1]   EFFECT OF INTERNAL VIRAL SEQUENCES ON THE UTILITY OF RETROVIRAL VECTORS [J].
ARMENTANO, D ;
YU, SF ;
KANTOFF, PW ;
VONRUDEN, T ;
ANDERSON, WF ;
GILBOA, E .
JOURNAL OF VIROLOGY, 1987, 61 (05) :1647-1650
[2]   MONOCLONAL-ANTIBODIES AGAINST HUMAN BETA-GLUCOCEREBROSIDASE [J].
BARNEVELD, RA ;
TEGELAERS, FPW ;
GINNS, EI ;
VISSER, P ;
LAANEN, EA ;
BRADY, RO ;
GALJAARD, H ;
BARRANGER, JA ;
REUSER, AJJ ;
TAGER, JM .
EUROPEAN JOURNAL OF BIOCHEMISTRY, 1983, 134 (03) :585-589
[3]  
Barranger J. A., 1989, METABOLIC BASIS INHE, P1677
[4]   COMBINATION OF INTERLEUKIN-3 AND INTERLEUKIN-6 PRESERVES STEM-CELL FUNCTION IN CULTURE AND ENHANCES RETROVIRUS-MEDIATED GENE-TRANSFER INTO HEMATOPOIETIC STEM-CELLS [J].
BODINE, DM ;
KARLSSON, S ;
NIENHUIS, AW .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1989, 86 (22) :8897-8901
[5]   METABOLISM OF GLUCOCEREBROSIDES .2. EVIDENCE OF AN ENZYMATIC DEFICIENCY IN GAUCHERS DISEASE [J].
BRADY, RO ;
KANFER, JN ;
SHAPIRO, D .
BIOCHEMICAL AND BIOPHYSICAL RESEARCH COMMUNICATIONS, 1965, 18 (02) :221-&
[6]   ISOLATION OF BIOLOGICALLY-ACTIVE RIBONUCLEIC-ACID FROM SOURCES ENRICHED IN RIBONUCLEASE [J].
CHIRGWIN, JM ;
PRZYBYLA, AE ;
MACDONALD, RJ ;
RUTTER, WJ .
BIOCHEMISTRY, 1979, 18 (24) :5294-5299
[7]   SINGLE-STEP METHOD OF RNA ISOLATION BY ACID GUANIDINIUM THIOCYANATE PHENOL CHLOROFORM EXTRACTION [J].
CHOMCZYNSKI, P ;
SACCHI, N .
ANALYTICAL BIOCHEMISTRY, 1987, 162 (01) :156-159
[8]   THE MOLECULAR-BIOLOGY OF GAUCHER DISEASE AND THE POTENTIAL FOR GENE-THERAPY [J].
CHOUDARY, PV ;
TSUJI, S ;
MARTIN, BM ;
GUILD, BC ;
MULLIGAN, RC ;
MURRAY, GJ ;
BARRANGER, JA ;
GINNS, EI .
COLD SPRING HARBOR SYMPOSIA ON QUANTITATIVE BIOLOGY, 1986, 51 :1047-1052
[9]   INTRODUCTION OF A SELECTABLE GENE INTO PRIMITIVE STEM-CELLS CAPABLE OF LONG-TERM RECONSTITUTION OF THE HEMATOPOIETIC SYSTEM OF W/WV MICE [J].
DICK, JE ;
MAGLI, MC ;
HUSZAR, D ;
PHILLIPS, RA ;
BERNSTEIN, A .
CELL, 1985, 42 (01) :71-79
[10]   LINEAGE-SPECIFIC EXPRESSION OF A HUMAN BETA-GLOBIN GENE IN MURINE BONE-MARROW TRANSPLANT RECIPIENTS RECONSTITUTED WITH RETROVIRUS-TRANSDUCED STEM-CELLS [J].
DZIERZAK, EA ;
PAPAYANNOPOULOU, T ;
MULLIGAN, RC .
NATURE, 1988, 331 (6151) :35-41