RIBOZYMES AS HUMAN THERAPEUTIC AGENTS

被引:107
作者
CHRISTOFFERSEN, RE
MARR, JJ
机构
[1] Ribozyme Pharmaceuticals, Inc., Boulder
关键词
D O I
10.1021/jm00012a001
中图分类号
R914 [药物化学];
学科分类号
100701 ;
摘要
[No abstract available]
引用
收藏
页码:2023 / 2037
页数:15
相关论文
共 131 条
[1]   ISOLATION OF NEW RIBOZYMES FROM A LARGE POOL OF RANDOM SEQUENCES [J].
BARTEL, DP ;
SZOSTAK, JW .
SCIENCE, 1993, 261 (5127) :1411-1418
[2]   TRANSLOCATION OF C-ABL ONCOGENE CORRELATES WITH THE PRESENCE OF A PHILADELPHIA-CHROMOSOME IN CHRONIC MYELOCYTIC-LEUKEMIA [J].
BARTRAM, CR ;
DEKLEIN, A ;
HAGEMEIJER, A ;
VANAGTHOVEN, T ;
VANKESSEL, AG ;
BOOTSMA, D ;
GROSVELD, G ;
FERGUSONSMITH, MA ;
DAVIES, T ;
STONE, M ;
HEISTERKAMP, N ;
STEPHENSON, JR ;
GROFFEN, J .
NATURE, 1983, 306 (5940) :277-280
[3]   THE SYNTHESIS OF MODIFIED OLIGONUCLEOTIDES BY THE PHOSPHORAMIDITE APPROACH AND THEIR APPLICATIONS [J].
BEAUCAGE, SL ;
IYER, RP .
TETRAHEDRON, 1993, 49 (28) :6123-6194
[4]   DIRECTED EVOLUTION OF AN RNA ENZYME [J].
BEAUDRY, AA ;
JOYCE, GF .
SCIENCE, 1992, 257 (5070) :635-641
[5]   SYNTHESIS OF 1-DEOXY-D-RIBOFURANOSE PHOSPHORAMIDITE AND THE INCORPORATION OF ABASIC NUCLEOTIDES IN STEM-LOOP-II OF A HAMMERHEAD RIBOZYME [J].
BEIGELMAN, L ;
KARPEISKY, A ;
USMAN, N .
BIOORGANIC & MEDICINAL CHEMISTRY LETTERS, 1994, 4 (14) :1715-1720
[6]  
BERINSTEIN N, 1987, CANCER RES, V47, P5954
[7]   FACILITATION OF HAMMERHEAD RIBOZYME CATALYSIS BY THE NUCLEOCAPSID PROTEIN OF HIV-1 AND THE HETEROGENEOUS NUCLEAR RIBONUCLEOPROTEIN A1 [J].
BERTRAND, EL ;
ROSSI, JJ .
EMBO JOURNAL, 1994, 13 (12) :2904-2912
[8]   EFFICIENT TRANS-CLEAVAGE AND A COMMON STRUCTURAL MOTIF FOR THE RIBOZYMES OF THE HUMAN HEPATITIS-DELTA AGENT [J].
BRANCH, AD ;
ROBERTSON, HD .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1991, 88 (22) :10163-10167
[9]   SPECIFIC GENE SUPPRESSION BY ENGINEERED RIBOZYMES IN MONKEY CELLS [J].
CAMERON, FH ;
JENNINGS, PA .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1989, 86 (23) :9139-9143
[10]   RIBOZYME CLEAVES REX TAX MESSENGER-RNA AND INHIBITS BOVINE LEUKEMIA-VIRUS EXPRESSION [J].
CANTOR, GH ;
MCELWAIN, TF ;
BIRKEBAK, TA ;
PALMER, GH .
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA, 1993, 90 (23) :10932-10936