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GENE-THERAPY ON THE SLY
被引:7
作者
:
SLY, WS
论文数:
0
引用数:
0
h-index:
0
机构:
Department of Biochemistry and Molecular Biology, Saint Louis University Medical Center, St. Louis, MO
SLY, WS
机构
:
[1]
Department of Biochemistry and Molecular Biology, Saint Louis University Medical Center, St. Louis, MO
来源
:
NATURE GENETICS
|
1993年
/ 4卷
/ 02期
关键词
:
D O I
:
10.1038/ng0693-105
中图分类号
:
Q3 [遗传学];
学科分类号
:
071007 ;
090102 ;
摘要
:
[No abstract available]
引用
收藏
页码:105 / 106
页数:2
相关论文
共 16 条
[1]
MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII - CHARACTERIZATION OF A MOUSE WITH BETA-GLUCURONIDASE DEFICIENCY
BIRKENMEIER, EH
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
BIRKENMEIER, EH
DAVISSON, MT
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
DAVISSON, MT
BEAMER, WG
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
BEAMER, WG
GANSCHOW, RE
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
GANSCHOW, RE
VOGLER, CA
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
VOGLER, CA
GWYNN, B
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
GWYNN, B
LYFORD, KA
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
LYFORD, KA
MALTAIS, LM
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
MALTAIS, LM
WAWRZYNIAK, CJ
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
WAWRZYNIAK, CJ
[J].
JOURNAL OF CLINICAL INVESTIGATION,
1989,
83
(04)
: 1258
-
1266
[2]
BIRKENMEIER EH, 1991, BLOOD, V78, P3081
[3]
IN-VITRO CORRECTION OF DEFICIENT HUMAN FIBROBLASTS BY BETA-GLUCURONIDASE FROM DIFFERENT HUMAN SOURCES
BROT, FE
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, SCH MED, DEPT PEDIAT, ST LOUIS, MO 63110 USA
BROT, FE
GLASER, JH
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, SCH MED, DEPT PEDIAT, ST LOUIS, MO 63110 USA
GLASER, JH
ROOZEN, KJ
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, SCH MED, DEPT PEDIAT, ST LOUIS, MO 63110 USA
ROOZEN, KJ
SLY, WS
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, SCH MED, DEPT PEDIAT, ST LOUIS, MO 63110 USA
SLY, WS
[J].
BIOCHEMICAL AND BIOPHYSICAL RESEARCH COMMUNICATIONS,
1974,
57
(01)
: 1
-
8
[4]
HURLER AND HUNTER SYNDROMES - MUTUAL CORRECTION OF DEFECT IN CULTURED FIBROBLASTS
FRATANTONI, JC
论文数:
0
引用数:
0
h-index:
0
FRATANTONI, JC
HALL, CW
论文数:
0
引用数:
0
h-index:
0
HALL, CW
NEUFELD, EF
论文数:
0
引用数:
0
h-index:
0
NEUFELD, EF
[J].
SCIENCE,
1968,
162
(3853)
: 570
-
+
[5]
GLASER JH, 1973, J LAB CLIN MED, V82, P969
[6]
BETA-GLUCURONIDASE DEFICIENCY MUCOPOLYSACCHARIDOSIS - STUDIES IN CULTURED FIBROBLASTS
HALL, CW
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
HALL, CW
CANTZ, M
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
CANTZ, M
NEUFELD, EF
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
NEUFELD, EF
[J].
ARCHIVES OF BIOCHEMISTRY AND BIOPHYSICS,
1973,
155
(01)
: 32
-
38
[7]
PHOSPHOHEXOSYL COMPONENTS OF A LYSOSOMAL ENZYME ARE RECOGNIZED BY PINOCYTOSIS RECEPTORS ON HUMAN FIBROBLASTS
KAPLAN, A
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, DEPT PEDIAT, DIV MED GENET, ST LOUIS, MO 63110 USA
KAPLAN, A
ACHORD, DT
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, DEPT PEDIAT, DIV MED GENET, ST LOUIS, MO 63110 USA
ACHORD, DT
SLY, WS
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, DEPT PEDIAT, DIV MED GENET, ST LOUIS, MO 63110 USA
SLY, WS
[J].
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
1977,
74
(05)
: 2026
-
2030
[8]
TRAFFICKING OF LYSOSOMAL-ENZYMES
KORNFELD, S
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV,SCH MED,DEPT BIOL CHEM,ST LOUIS,MO 63110
WASHINGTON UNIV,SCH MED,DEPT BIOL CHEM,ST LOUIS,MO 63110
KORNFELD, S
[J].
FASEB JOURNAL,
1987,
1
(06)
: 462
-
468
[9]
CORRECTION OF LYSOSOMAL STORAGE IN THE LIVER AND SPLEEN OF MPS-VII MICE BY IMPLANTATION OF GENETICALLY-MODIFIED SKIN FIBROBLASTS
MOULLIER, P
论文数:
0
引用数:
0
h-index:
0
机构:
INST PASTEUR,RETROVIRUS & TRANSFERT GENET LAB,25 RUE DR ROUX,F-75724 PARIS 15,FRANCE
MOULLIER, P
BOHL, D
论文数:
0
引用数:
0
h-index:
0
机构:
INST PASTEUR,RETROVIRUS & TRANSFERT GENET LAB,25 RUE DR ROUX,F-75724 PARIS 15,FRANCE
BOHL, D
HEARD, JM
论文数:
0
引用数:
0
h-index:
0
机构:
INST PASTEUR,RETROVIRUS & TRANSFERT GENET LAB,25 RUE DR ROUX,F-75724 PARIS 15,FRANCE
HEARD, JM
DANOS, O
论文数:
0
引用数:
0
h-index:
0
机构:
INST PASTEUR,RETROVIRUS & TRANSFERT GENET LAB,25 RUE DR ROUX,F-75724 PARIS 15,FRANCE
DANOS, O
[J].
NATURE GENETICS,
1993,
4
(02)
: 154
-
159
[10]
INHERITED DISORDERS OF LYSOSOMAL METABOLISM
NEUFELD, EF
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
NEUFELD, EF
LIM, TW
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
LIM, TW
SHAPIRO, LJ
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
SHAPIRO, LJ
[J].
ANNUAL REVIEW OF BIOCHEMISTRY,
1975,
44
: 357
-
376
←
1
2
→
共 16 条
[1]
MURINE MUCOPOLYSACCHARIDOSIS TYPE-VII - CHARACTERIZATION OF A MOUSE WITH BETA-GLUCURONIDASE DEFICIENCY
BIRKENMEIER, EH
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
BIRKENMEIER, EH
DAVISSON, MT
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
DAVISSON, MT
BEAMER, WG
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
BEAMER, WG
GANSCHOW, RE
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
GANSCHOW, RE
VOGLER, CA
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
VOGLER, CA
GWYNN, B
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
GWYNN, B
LYFORD, KA
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
LYFORD, KA
MALTAIS, LM
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
MALTAIS, LM
WAWRZYNIAK, CJ
论文数:
0
引用数:
0
h-index:
0
机构:
CHILDRENS HOSP RES FDN,DIV BASIC SCI RES,CINCINNATI,OH 45229
WAWRZYNIAK, CJ
[J].
JOURNAL OF CLINICAL INVESTIGATION,
1989,
83
(04)
: 1258
-
1266
[2]
BIRKENMEIER EH, 1991, BLOOD, V78, P3081
[3]
IN-VITRO CORRECTION OF DEFICIENT HUMAN FIBROBLASTS BY BETA-GLUCURONIDASE FROM DIFFERENT HUMAN SOURCES
BROT, FE
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, SCH MED, DEPT PEDIAT, ST LOUIS, MO 63110 USA
BROT, FE
GLASER, JH
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, SCH MED, DEPT PEDIAT, ST LOUIS, MO 63110 USA
GLASER, JH
ROOZEN, KJ
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, SCH MED, DEPT PEDIAT, ST LOUIS, MO 63110 USA
ROOZEN, KJ
SLY, WS
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, SCH MED, DEPT PEDIAT, ST LOUIS, MO 63110 USA
SLY, WS
[J].
BIOCHEMICAL AND BIOPHYSICAL RESEARCH COMMUNICATIONS,
1974,
57
(01)
: 1
-
8
[4]
HURLER AND HUNTER SYNDROMES - MUTUAL CORRECTION OF DEFECT IN CULTURED FIBROBLASTS
FRATANTONI, JC
论文数:
0
引用数:
0
h-index:
0
FRATANTONI, JC
HALL, CW
论文数:
0
引用数:
0
h-index:
0
HALL, CW
NEUFELD, EF
论文数:
0
引用数:
0
h-index:
0
NEUFELD, EF
[J].
SCIENCE,
1968,
162
(3853)
: 570
-
+
[5]
GLASER JH, 1973, J LAB CLIN MED, V82, P969
[6]
BETA-GLUCURONIDASE DEFICIENCY MUCOPOLYSACCHARIDOSIS - STUDIES IN CULTURED FIBROBLASTS
HALL, CW
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
HALL, CW
CANTZ, M
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
CANTZ, M
NEUFELD, EF
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
NEUFELD, EF
[J].
ARCHIVES OF BIOCHEMISTRY AND BIOPHYSICS,
1973,
155
(01)
: 32
-
38
[7]
PHOSPHOHEXOSYL COMPONENTS OF A LYSOSOMAL ENZYME ARE RECOGNIZED BY PINOCYTOSIS RECEPTORS ON HUMAN FIBROBLASTS
KAPLAN, A
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, DEPT PEDIAT, DIV MED GENET, ST LOUIS, MO 63110 USA
KAPLAN, A
ACHORD, DT
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, DEPT PEDIAT, DIV MED GENET, ST LOUIS, MO 63110 USA
ACHORD, DT
SLY, WS
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV, DEPT PEDIAT, DIV MED GENET, ST LOUIS, MO 63110 USA
SLY, WS
[J].
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
1977,
74
(05)
: 2026
-
2030
[8]
TRAFFICKING OF LYSOSOMAL-ENZYMES
KORNFELD, S
论文数:
0
引用数:
0
h-index:
0
机构:
WASHINGTON UNIV,SCH MED,DEPT BIOL CHEM,ST LOUIS,MO 63110
WASHINGTON UNIV,SCH MED,DEPT BIOL CHEM,ST LOUIS,MO 63110
KORNFELD, S
[J].
FASEB JOURNAL,
1987,
1
(06)
: 462
-
468
[9]
CORRECTION OF LYSOSOMAL STORAGE IN THE LIVER AND SPLEEN OF MPS-VII MICE BY IMPLANTATION OF GENETICALLY-MODIFIED SKIN FIBROBLASTS
MOULLIER, P
论文数:
0
引用数:
0
h-index:
0
机构:
INST PASTEUR,RETROVIRUS & TRANSFERT GENET LAB,25 RUE DR ROUX,F-75724 PARIS 15,FRANCE
MOULLIER, P
BOHL, D
论文数:
0
引用数:
0
h-index:
0
机构:
INST PASTEUR,RETROVIRUS & TRANSFERT GENET LAB,25 RUE DR ROUX,F-75724 PARIS 15,FRANCE
BOHL, D
HEARD, JM
论文数:
0
引用数:
0
h-index:
0
机构:
INST PASTEUR,RETROVIRUS & TRANSFERT GENET LAB,25 RUE DR ROUX,F-75724 PARIS 15,FRANCE
HEARD, JM
DANOS, O
论文数:
0
引用数:
0
h-index:
0
机构:
INST PASTEUR,RETROVIRUS & TRANSFERT GENET LAB,25 RUE DR ROUX,F-75724 PARIS 15,FRANCE
DANOS, O
[J].
NATURE GENETICS,
1993,
4
(02)
: 154
-
159
[10]
INHERITED DISORDERS OF LYSOSOMAL METABOLISM
NEUFELD, EF
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
NEUFELD, EF
LIM, TW
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
LIM, TW
SHAPIRO, LJ
论文数:
0
引用数:
0
h-index:
0
机构:
NIAMDD,BETHESDA,MD 20014
NIAMDD,BETHESDA,MD 20014
SHAPIRO, LJ
[J].
ANNUAL REVIEW OF BIOCHEMISTRY,
1975,
44
: 357
-
376
←
1
2
→