Genome Editing in Retinal Diseases using CRISPR Technology

被引：11

作者：

Yiu, Glenn ^{[1
]}

机构：

[1] Univ Calif Davis, Dept Ophthalmol & Vis Sci, Sacramento, CA 95817 USA

来源：

OPHTHALMOLOGY RETINA | 2018年 / 2卷 / 01期

关键词：

D O I：

10.1016/j.oret.2017.09.015

中图分类号：

R77 [眼科学];

学科分类号：

100212 ;

摘要：

引用

页码：1 / 3

页数：3

共 21 条

[1] Long-Term Effect of Gene Therapy on Leber's Congenital Amaurosis [J].

Bainbridge, J. W. B. ;

Mehat, M. S. ;

Sundaram, V. ;

Robbie, S. J. ;

Barker, S. E. ;

Ripamonti, C. ;

Georgiadis, A. ;

Mowat, F. M. ;

Beattie, S. G. ;

Gardner, P. J. ;

Feathers, K. L. ;

Luong, V. A. ;

Yzer, S. ;

Balaggan, K. ;

Viswanathan, A. ;

de Ravel, T. J. L. ;

Casteels, I. ;

Holder, G. E. ;

Tyler, N. ;

Fitzke, F. W. ;

Weleber, R. G. ;

Nardini, M. ;

Moore, A. T. ;

Thompson, D. A. ;

Petersen-Jones, S. M. ;

Michaelides, M. ;

van den Born, L. I. ;

Stockman, A. ;

Smith, A. J. ;

Rubin, G. ;

Ali, R. R. .

NEW ENGLAND JOURNAL OF MEDICINE, 2015, 372 (20) :1887-1897

[2] In Vivo CRISPR/Cas9 Gene Editing Corrects Retinal Dystrophy in the S334ter-3 Rat Model of Autosomal Dominant Retinitis Pigmentosa [J].

Bakondi, Benjamin ;

Lv, Wenjian ;

Lui, Bin ;

Jones, Melissa K. ;

Tsai, Yuchun ;

Kim, Kevin J. ;

Levy, Rachelle ;

Akhtar, Aslam Abbasi ;

Breunig, Joshua J. ;

Svendseni, Clive N. ;

Wang, Shaomei .

MOLECULAR THERAPY, 2016, 24 (03) :556-563

[3] Precision Medicine: Genetic Repair of Retinitis Pigmentosa in Patient-Derived Stem Cells [J].

Bassuk, Alexander G. ;

Zheng, Andrew ;

Li, Yao ;

Tsang, Stephen H. ;

Mahajan, Vinit B. .

SCIENTIFIC REPORTS, 2016, 6

[4] Analysis of off-target effects of CRISPR/Cas-derived RNA-guided endonucleases and nickases [J].

Cho, Seung Woo ;

Kim, Sojung ;

Kim, Yongsub ;

Kweon, Jiyeon ;

Kim, Heon Seok ;

Bae, Sangsu ;

Kim, Jin-Soo .

GENOME RESEARCH, 2014, 24 (01) :132-141

[5] Multiplex Genome Engineering Using CRISPR/Cas Systems [J].

Cong, Le ;

Ran, F. Ann ;

Cox, David ;

Lin, Shuailiang ;

Barretto, Robert ;

Habib, Naomi ;

Hsu, Patrick D. ;

Wu, Xuebing ;

Jiang, Wenyan ;

Marraffini, Luciano A. ;

Zhang, Feng .

SCIENCE, 2013, 339 (6121) :819-823

[6] High-frequency off-target mutagenesis induced by CRISPR-Cas nucleases in human cells [J].

Fu, Yanfang ;

Foden, Jennifer A. ;

Khayter, Cyd ;

Maeder, Morgan L. ;

Reyon, Deepak ;

Joung, J. Keith ;

Sander, Jeffry D. .

NATURE BIOTECHNOLOGY, 2013, 31 (09) :822-+

[7] Genome editing abrogates angiogenesis in vivo [J].

Huang, Xionggao ;

Zhou, Guohong ;

Wu, Wenyi ;

Duan, Yajian ;

Ma, Gaoen ;

Song, Jingyuan ;

Xiao, Ru ;

Vandenberghe, Luk ;

Zhang, Feng ;

D'Amore, Patricia A. ;

Lei, Hetian .

NATURE COMMUNICATIONS, 2017, 8

[8] Editing VEGFR2 Blocks VEGF-Induced Activation of Akt and Tube Formation [J].

Huang, Xionggao ;

Zhou, Guohong ;

Wu, Wenyi ;

Ma, Gaoen ;

D'Amore, Patricia A. ;

Mukai, Shizuo ;

Lei, Hetian .

INVESTIGATIVE OPHTHALMOLOGY & VISUAL SCIENCE, 2017, 58 (02) :1228-1236

[9] Improvement and Decline in Vision with Gene Therapy in Childhood Blindness [J].

Jacobson, Samuel G. ;

Cideciyan, Artur V. ;

Roman, Alejandro J. ;

Sumaroka, Alexander ;

Schwartz, Sharon B. ;

Heon, Elise ;

Hauswirth, William W. .

NEW ENGLAND JOURNAL OF MEDICINE, 2015, 372 (20) :1920-1926

[10] A Programmable Dual-RNA-Guided DNA Endonuclease in Adaptive Bacterial Immunity [J].

Jinek, Martin ;

Chylinski, Krzysztof ;

Fonfara, Ines ;

Hauer, Michael ;

Doudna, Jennifer A. ;

Charpentier, Emmanuelle .

SCIENCE, 2012, 337 (6096) :816-821

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