Longitudinal prospective cohort study to assess peripheral motor function with extensive electrophysiological techniques in patients with Spinal Muscular Atrophy (SMA): the SMA Motor Map protocol

被引:0
作者
Leandra A. A. Ros
H. Stephan Goedee
Hessel Franssen
Fay-Lynn Asselman
Bart Bartels
Inge Cuppen
Ruben P. A. van Eijk
Boudewijn T. H. M. Sleutjes
W. Ludo van der Pol
Renske I. Wadman
机构
[1] University Medical Center Utrecht,Department of Neurology & Neurosurgery
[2] UMC Utrecht Brain Center,Child Development and Exercise Centre
[3] Utrecht University,Biostatistics and Research Support, Julius Center for Health Sciences and Primary Care
[4] Wilhelmina Children’s Hospital,undefined
[5] University Medical Center Utrecht,undefined
[6] Utrecht University,undefined
[7] University Medical Center Utrecht,undefined
[8] Utrecht University,undefined
来源
BMC Neurology | / 23卷
关键词
Spinal muscular atrophy; Nusinersen; Risdiplam; Electrophysiological techniques; Motor unit;
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