Orphan drugs, orphan diseases. The first decade of orphan drug legislation in the EU

被引：0
|
作者：
Roberta Joppi
Vittorio Bertele’
Silvio Garattini
机构：
[1] Mario Negri Institute for Pharmacological Research,Laboratory of Drug Regulatory Policies
[2] Local Health Unit of Verona,Pharmaceutical Department
来源：
European Journal of Clinical Pharmacology | 2013年 / 69卷
关键词：
Orphan drug; Rare disease; Pharmacological research; Drug regulation; Development; Preclinical studies; Clinical trials; Clinical efficacy; Placebo; Outcome measures;
D O I：
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中图分类号：
学科分类号：
摘要：
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收藏
页码：1009 / 1024
页数：15
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