Molecular Therapies for Muscular Dystrophies

被引：0
作者：
Ava Y. Lin
Leo H. Wang
机构：
[1] University of Washington,Department of Neurology
来源：
Current Treatment Options in Neurology | 2018年 / 20卷
关键词：
Limb-girdle muscular dystrophy; Muscular dystrophy; Therapies; Molecular therapies; Gene therapy;
D O I：
暂无
中图分类号：
学科分类号：
摘要：
引用
收藏
相关论文
共 50 条
  • [31] Dystrophinopathies and Limb-Girdle Muscular Dystrophies
    Domingos, Joana
    Sarkozy, Anna
    Scoto, Mariacristina
    Muntoni, Francesco
    NEUROPEDIATRICS, 2017, 48 (04) : 262 - 272
  • [32] Expression profiling in the muscular dystrophies: Identification of novel aspects of molecular pathophysiology
    Chen, YW
    Zhao, P
    Borup, R
    Hoffman, EP
    JOURNAL OF CELL BIOLOGY, 2000, 151 (06) : 1321 - 1336
  • [33] Limb-girdle muscular dystrophies - from genetics to molecular pathology
    Laval, SH
    Bushby, KMD
    NEUROPATHOLOGY AND APPLIED NEUROBIOLOGY, 2004, 30 (02) : 91 - 105
  • [34] In Vivo Genome Engineering for the Treatment of Muscular Dystrophies
    Kustermann, Monika
    Rok, Matthew J.
    Cohn, Ronald D.
    Ivakine, Evgueni A.
    CURRENT STEM CELL REPORTS, 2020, 6 (03) : 52 - 66
  • [35] Hereditary muscular dystrophies and the heart
    Hermans, M. C. E.
    Pinto, Y. M.
    Merkies, I. S. J.
    de Die-Smulders, C. E. M.
    Crijns, H. J. G. M.
    Faber, C. G.
    NEUROMUSCULAR DISORDERS, 2010, 20 (08) : 479 - 492
  • [36] Inherited myopathies and muscular dystrophies
    Cardamone, Michael
    Darras, Basil T.
    Ryan, Monique M.
    SEMINARS IN NEUROLOGY, 2008, 28 (02) : 250 - 259
  • [37] Cardiac involvement in the muscular dystrophies
    Silvestri, Nicholas J.
    Ismail, Haisam
    Zimetbaum, Peter
    Raynor, Elizabeth M.
    MUSCLE & NERVE, 2018, 57 (05) : 707 - 715
  • [38] Cardiac manifestations of muscular dystrophies
    Perrot, A
    Spuler, S
    Geier, C
    Dietz, R
    Osterziel, KJ
    ZEITSCHRIFT FUR KARDIOLOGIE, 2005, 94 (05): : 312 - +
  • [39] Cardiac manifestations of muscular dystrophies
    Perrot A.
    Spuler S.
    Geier C.
    Dietz R.
    Osterziel K.J.
    Zeitschrift für Kardiologie, 2005, 94 (5): : 312 - 320
  • [40] Limb girdle muscular dystrophies
    Finsterer, J
    NERVENARZT, 2004, 75 (12): : 1153 - +
12345