Genetic therapy for spinal muscular atrophy

被引:0
作者
Alex MacKenzie
机构
[1] Alex MacKenzie is at the Children's Hospital of Eastern Ontario Research Institute,
[2] University of Ottawa,undefined
[3] Ottawa,undefined
[4] Ontario,undefined
[5] Canada.,undefined
来源
Nature Biotechnology | 2010年 / 28卷
关键词
D O I
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中图分类号
学科分类号
摘要
A severe inherited neuromuscular disease is corrected in mice by intravenous gene delivery.
引用
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页码:235 / 237
页数:2
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