Genetic therapy for spinal muscular atrophy

被引：0
作者：
Alex MacKenzie
机构：
[1] Alex MacKenzie is at the Children's Hospital of Eastern Ontario Research Institute,
[2] University of Ottawa,undefined
[3] Ottawa,undefined
[4] Ontario,undefined
[5] Canada.,undefined
来源：
Nature Biotechnology | 2010年 / 28卷
关键词：
D O I：
暂无
中图分类号：
学科分类号：
摘要：
A severe inherited neuromuscular disease is corrected in mice by intravenous gene delivery.
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页码：235 / 237
页数：2
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