Antibody-mediated enzyme replacement therapy targeting both lysosomal and cytoplasmic glycogen in Pompe disease

被引：0

作者：

Haiqing Yi

Tao Sun

Dustin Armstrong

Scott Borneman

Chunyu Yang

Stephanie Austin

Priya S. Kishnani

Baodong Sun

机构：

[1] Duke University School of Medicine,Division of Medical Genetics, Department of Pediatrics

[2] Valerion Therapeutics,undefined

[3] Borneman Consulting,undefined

来源：

Journal of Molecular Medicine | 2017年 / 95卷

关键词：

Pompe disease; 3E10 Fab; Enzyme replacement therapy; Recombinant human acid α-glucosidase; Fusion protein; Cytoplasmic glycogen;

D O I：

暂无

中图分类号：

学科分类号：

摘要：

引用

页码：513 / 521

页数：8

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