Efficacy of tocilizumab therapy in a patient with severe pancytopenia associated with a STAT3 gain-of-function mutation

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作者：
Wenjie Wang
Luyao Liu
Xiaoying Hui
Ying Wang
Wenjing Ying
Qinhua Zhou
Jia Hou
Mi Yang
Bijun Sun
Jinqiao Sun
Xiaochuan Wang
机构：
[1] Children’s Hospital of Fudan University,Department of Clinical Immunology
[2] National Children’s Medical Center,undefined
来源：
BMC Immunology | / 22卷
关键词：
STAT3 transcription factor; Tocilizumab; Immune Dysregulation; Gain-of-function mutations;
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