Matching-Adjusted Indirect Comparison of Recombinant Factor IX Albumin Fusion Protein Versus Recombinant Factor IX Fc Fusion Protein for Weekly Prophylactic Treatment of Hemophilia B

被引:0
作者
Benoit Guillet
Songkai Yan
Becky Hooper
Douglass Drelich
Jason Steenkamp
Radovan Tomic
Maria Elisa Mancuso
机构
[1] Hemophilia Treatment Center of Rennes-Bretagne,
[2] University Hospital Center (CHU) Rennes,undefined
[3] CSL Behring,undefined
[4] EVERSANA,undefined
[5] CSL Behring,undefined
[6] IRCCS Humanitas Research Hospital and Humanitas University,undefined
来源
Advances in Therapy | 2024年 / 41卷
关键词
Efficacy; Hemophilia B; Matching-adjusted indirect comparisons; Prophylactic treatment; Recombinant factor IX albumin fusion protein; Recombinant factor IX Fc fusion protein;
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学科分类号
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页码:649 / 658
页数:9
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[21]   Biodistribution of the recombinant fusion protein linking coagulation factor IX with albumin (rIX-FP) in rats [J].
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