Patient-reported burden of hereditary transthyretin amyloidosis on functioning and well-being

被引:0
作者
Andrew Lovley
Kimberly Raymond
Spencer D. Guthrie
Michael Pollock
Vaishali Sanchorawala
Michelle K. White
机构
[1] QualityMetric Incorporated,Amyloidosis Center
[2] Aurora Bio,undefined
[3] Akcea Therapeutics,undefined
[4] Boston University School of Medicine and Boston Medical Center,undefined
来源
Journal of Patient-Reported Outcomes | / 5卷
关键词
Amyloidosis; Burden of disease; Quality of life; Patient interviews; Qualitative; Rare disease;
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