Differing clinical features between Japanese siblings with cerebrotendinous xanthomatosis with a novel compound heterozygous CYP27A1 mutation: a case report

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作者
Shingo Koyama
Yuma Okabe
Yuya Suzuki
Ryosuke Igari
Hiroyasu Sato
Chifumi Iseki
Kazuyo Tanji
Kyoko Suzuki
Yasuyuki Ohta
机构
[1] Yamagata University Faculty of Medicine,Department of Internal Medicine III, Division of Neurology and Clinical Neuroscience
[2] Yamagata University Faculty of Medicine,Department of Clinical Neuroscience
[3] Koishikawa Tokyo Hospital,Department of Psychiatry
[4] Tohoku University Graduate School of Medicine,Department of Behavioral Neurology and Cognitive Neuroscience
来源
BMC Neurology | / 22卷
关键词
CTX; CYP27A1; Cholestanol; Chenodeoxycholic acid; Case report;
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