Unmet clinical needs and burden in Angelman syndrome: a review of the literature

被引：0
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作者：
Anne C. Wheeler
Patricia Sacco
Raquel Cabo
机构：
[1] RTI International,
[2] RTI Health Solutions,undefined
[3] Ovid Therapeutics Inc.,undefined
来源：
Orphanet Journal of Rare Diseases | / 12卷
关键词：
Angleman syndrome; Burden; Unmet clinical needs; Clinical features; Treatments;
D O I：
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