In Vivo Genome Engineering for the Treatment of Muscular Dystrophies

被引：0
作者：
Monika Kustermann
Matthew J. Rok
Ronald D. Cohn
Evgueni A. Ivakine
机构：
[1] Peter Gilgan Centre for Research and Learning,Program in Genetics and Genome Biology
[2] The Hospital for Sick Children Research Institute,Department of Molecular Genetics
[3] University of Toronto,Department of Pediatrics
[4] The Hospital for Sick Children,Institute of Medical Science
[5] University of Toronto,Department of Physiology
[6] University of Toronto,undefined
来源：
Current Stem Cell Reports | 2020年 / 6卷
关键词：
Muscular dystrophy; Duchenne muscular dystrophy; Genome editing; CRISPR/Cas9; Adeno-associated viruses; Nanoparticles;
D O I：
暂无
中图分类号：
学科分类号：
摘要：
引用
收藏
页码：52 / 66
页数：14
相关论文
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