Update on enzyme replacement therapy (ert) with recombinant human arylsulfatase b (rhasb) for mps vi (maroteaux-lamy): 169

被引:0
作者
Harmatz P. [1 ]
Giugliani R. [1 ]
Schwartz I. [2 ]
Guffon N. [3 ]
Miranda C. [3 ]
Teles E. [3 ]
Wraith J.E. [4 ]
Beck M. [4 ]
Scarpa M. [5 ]
Yu Z.-F. [5 ]
Wittes J. [6 ]
Berger K. [6 ]
Newman M. [6 ]
机构
[1] CHILDREN'S HOSPITAL OAKLAND,DEPARTMENT OF PEDIATRICS
[2] HOSPITAL DE CLINICAS DE PORTO,undefined
[3] HOPITAL EDOUARD HERRIOT,undefined
[4] INSTITUTO DE BIOLOGIA MOLECULAR E CELULAR AND HOSPITAL DE SAO JOAO,undefined
[5] ROYAL MANCHESTER CHILDREN'S HOSPITAL,undefined
[6] CHILDREN'S HOSPITAL,undefined
[7] UNIVERSITY OF MAINZ,undefined
[8] UNIVERSITY OF PADOVA,undefined
[9] STATISTICS COLLABORATIVE,undefined
[10] INC,undefined
[11] NYU SCHOOL OF MEDICINE,undefined
[12] BIOMARIN PHARMACEUTICAL INC,undefined
关键词
D O I
10.1203/00006450-200508000-00198
中图分类号
学科分类号
摘要
[No abstract available]
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页码:383 / 383
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