Arbaclofen in fragile X syndrome: results of phase 3 trials

被引：0
作者：
Elizabeth Berry-Kravis
Randi Hagerman
Jeannie Visootsak
Dejan Budimirovic
Walter E. Kaufmann
Maryann Cherubini
Peter Zarevics
Karen Walton-Bowen
Paul Wang
Mark F. Bear
Randall L. Carpenter
机构：
[1] Rush University Medical Center,Departments of Pediatrics, Neurological Sciences, Biochemistry
[2] University of California Davis Medical Center,MIND Institute and Department of Pediatrics
[3] Emory University,Department of Human Genetics
[4] Kennedy Krieger Institute,Departments of Psychiatry &Behavioral Sciences
[5] the Johns Hopkins Medical Institutions,Department of Neurology, Boston Children’s Hospital
[6] Boston,undefined
[7] MA 02115 and Greenwood Genetic Center,undefined
[8] Seaside Therapeutics Inc,undefined
[9] Simons Foundation Autism Research Initiative,undefined
[10] Autism Speaks,undefined
[11] The Picower Institute for Learning and Memory,undefined
[12] Massachusetts Institute of Technology,undefined
[13] Rett Syndrome Research Trust,undefined
来源：
Journal of Neurodevelopmental Disorders | 2017年 / 9卷
关键词：
Fragile X syndrome; Arbaclofen; GABA agonist; FMR1; Targeted treatment; Neurodevelopmental disorder;
D O I：
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中图分类号：
学科分类号：
摘要：
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