Gene therapy restores auditory and vestibular function in a mouse model of Usher syndrome type 1c

被引：0
作者：
Bifeng Pan
Charles Askew
Alice Galvin
Selena Heman-Ackah
Yukako Asai
Artur A Indzhykulian
Francine M Jodelka
Michelle L Hastings
Jennifer J Lentz
Luk H Vandenberghe
Jeffrey R Holt
Gwenaëlle S Géléoc
机构：
[1] F.M. Kirby Center for Neurobiology,Department of Otolaryngology
[2] Boston Children's Hospital,Department of Neurobiology
[3] Harvard Medical School,Department of Cell Biology & Anatomy
[4] Harvard Medical School,Department of Otorhinolaryngology & Bio
[5] Chicago Medical School,communications and Neuroscience Center
[6] Rosalind Franklin University of Medicine and Science,Department of Ophthalmology
[7] LSU Health Sciences Center,Department of Neurology
[8] Grousbeck Gene Therapy Center,undefined
[9] Schepens Eye Research Institute and Massachusetts Eye and Ear,undefined
[10] Harvard Medical School,undefined
[11] F.M. Kirby Center for Neurobiology,undefined
[12] Boston Children's Hospital,undefined
[13] Harvard Medical School,undefined
[14] Present addresses: Gene Therapy Center,undefined
[15] University of North Carolina,undefined
[16] Chapel Hill,undefined
[17] North Carolina,undefined
[18] USA (C.A.); MedStar Washington Hospital Center,undefined
[19] Georgetown University Medical Center,undefined
[20] Washington,undefined
[21] DC,undefined
[22] USA (S.H.-A.).,undefined
来源：
Nature Biotechnology | 2017年 / 35卷
关键词：
D O I：
暂无
中图分类号：
学科分类号：
摘要：
Gene therapy in the inner ear achieves unprecedented recovery of hearing and balance behavior in Usher syndrome mice.
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收藏
页码：264 / 272
页数：8
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