Clinical and molecular characteristics of 69 Chinese patients with ornithine transcarbamylase deficiency

被引:0
作者
Deyun Lu
Feng Han
Wenjuan Qiu
Huiwen Zhang
Jun Ye
Lili Liang
Yu Wang
Wenjun Ji
Xia Zhan
Xuefan Gu
Lianshu Han
机构
[1] Xinhua Hospital Affiliated To Shanghai Jiao Tong University School of Medicine,Department of Pediatric Endocrinology and Genetic Metabolism, Shanghai Institute for Pediatric Research
[2] National Children’s Medical Center,Department of Neurology, Shanghai Children’s Medical Center Affiliated to Shanghai Jiao Tong University School of Medicine
来源
Orphanet Journal of Rare Diseases | / 15卷
关键词
Hyperammonemia; Urea cycle disorders; Ornithine transcarbamylase deficiency; OTC; Gene mutation;
D O I
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中图分类号
学科分类号
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