RPE65-associated inherited retinal diseases: consensus recommendations for eligibility to gene therapy

被引:0
作者
Andrea Sodi
Sandro Banfi
Francesco Testa
Michele Della Corte
Ilaria Passerini
Elisabetta Pelo
Settimio Rossi
Francesca Simonelli
机构
[1] Careggi Teaching Hospital,Department of Ophthalmology
[2] University of Campania “Luigi Vanvitelli”,Medical Genetics, Department of Precision Medicine
[3] Telethon Institute of Genetics and Medicine (TIGEM),Eye Clinic, Multidisciplinary Department of Medical, Surgical and Dental Sciences
[4] University of Campania “Luigi Vanvitelli”,Department of Genetic Diagnosis
[5] Careggi Teaching Hospital,undefined
来源
Orphanet Journal of Rare Diseases | / 16卷
关键词
Gene therapy; Inherited retinal diseases; Voretigene neparvovec;
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