Defining clinical endpoints in limb girdle muscular dystrophy: a GRASP-LGMD study

被引:0
作者
Amy Doody
Lindsay Alfano
Jordi Diaz-Manera
Linda Lowes
Tahseen Mozaffar
Katherine D. Mathews
Conrad C. Weihl
Matthew Wicklund
Man Hung
Jeffrey Statland
Nicholas E. Johnson
机构
[1] Virginia Commonwealth University,
[2] Nationwide Children’s Hospital,undefined
[3] Newcastle University,undefined
[4] University of California,undefined
[5] University of Iowa Carver College of Medicine,undefined
[6] Washington University,undefined
[7] UT Health San Antonio,undefined
[8] Roseman University,undefined
[9] University of Kansas Medical Center,undefined
来源
BMC Neurology | / 24卷
关键词
Limb girdle muscular dystrophy; Muscular dystrophy; Clinical outcome assessments; Clinical trials; Therapeutic development;
D O I
暂无
中图分类号
学科分类号
摘要
引用
收藏
相关论文
共 239 条
  • [91] Keramaris E(undefined)undefined undefined undefined undefined-undefined
  • [92] Pei JL(undefined)undefined undefined undefined undefined-undefined
  • [93] Xiao X(undefined)undefined undefined undefined undefined-undefined
  • [94] Lu Q(undefined)undefined undefined undefined undefined-undefined
  • [95] Thomas PJ(undefined)undefined undefined undefined undefined-undefined
  • [96] Xu R(undefined)undefined undefined undefined undefined-undefined
  • [97] Martin PT(undefined)undefined undefined undefined undefined-undefined
  • [98] Vannoy CH(undefined)undefined undefined undefined undefined-undefined
  • [99] Leroy V(undefined)undefined undefined undefined undefined-undefined
  • [100] Lu QL(undefined)undefined undefined undefined undefined-undefined