Defining clinical endpoints in limb girdle muscular dystrophy: a GRASP-LGMD study

被引:0
作者
Amy Doody
Lindsay Alfano
Jordi Diaz-Manera
Linda Lowes
Tahseen Mozaffar
Katherine D. Mathews
Conrad C. Weihl
Matthew Wicklund
Man Hung
Jeffrey Statland
Nicholas E. Johnson
机构
[1] Virginia Commonwealth University,
[2] Nationwide Children’s Hospital,undefined
[3] Newcastle University,undefined
[4] University of California,undefined
[5] University of Iowa Carver College of Medicine,undefined
[6] Washington University,undefined
[7] UT Health San Antonio,undefined
[8] Roseman University,undefined
[9] University of Kansas Medical Center,undefined
来源
BMC Neurology | / 24卷
关键词
Limb girdle muscular dystrophy; Muscular dystrophy; Clinical outcome assessments; Clinical trials; Therapeutic development;
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