Longitudinal natural history of type I spinal muscular atrophy: a critical review

被引：0
作者：
Eugenio Mercuri
Simona Lucibello
Marco Perulli
Giorgia Coratti
Roberto de Sanctis
Maria Carmela Pera
Marika Pane
Jacqueline Montes
Darryl C. de Vivo
Basil T. Darras
Stephen J. Kolb
Richard S. Finkel
机构：
[1] Catholic University,Paediatric Neurology
[2] Fondazione Policlinico Universitario Agostino Gemelli IRCCS,Centro Clinico Nemo, Policlinico Gemelli
[3] Columbia University Medical Center,Departments of Rehabilitation and Regenerative Medicine
[4] Columbia University Medical Center,Department of Neurology
[5] Boston Children’s Hospital,Department of Neurology
[6] Harvard Medical School,Department of Neurology
[7] The Ohio State University Wexner Medical Center,Department of Biological Chemistry & Pharmacology
[8] The Ohio State University Wexner Medical Center,Nemours Children’s Hospital
[9] University of Central Florida College of Medicine,undefined
来源：
Orphanet Journal of Rare Diseases | / 15卷
关键词：
Spinal muscular atrophy; Natural history; CHOP INTEND;
D O I：
暂无
中图分类号：
学科分类号：
摘要：
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