Delivering efficient liver-directed AAV-mediated gene therapy

被引:0
作者
J Baruteau
S N Waddington
I E Alexander
P Gissen
机构
[1] Genetics and Genomic Medicine Programme,Department of Metabolic Medicine
[2] Great Ormond Street Institute of Child Health,undefined
[3] University College London,undefined
[4] Great Ormond Street Hospital for Children NHS Foundation Trust,undefined
[5] Maternal and Fetal Medicine,undefined
[6] Gene Transfer Technology Group,undefined
[7] Institute for Women’s Health,undefined
[8] University College London,undefined
[9] Antiviral Gene Therapy Research Unit,undefined
[10] Faculty of Health Sciences,undefined
[11] University of the Witswatersrand,undefined
[12] Gene Therapy Research Unit,undefined
[13] The Children’s Hospital at Westmead and Children’s Medical Research Institute,undefined
[14] Discipline of Child and Adolescent Health,undefined
[15] The University of Sydney,undefined
[16] MRC Laboratory for Molecular Biology,undefined
[17] University College London,undefined
来源
Gene Therapy | 2017年 / 24卷
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摘要
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页码:263 / 264
页数:1
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