Patient with multiple acyl-CoA dehydrogenase deficiency disease and ETFDH mutations benefits from riboflavin therapy: a case report

被引:0
作者
Liuh Ling Goh
Yingshan Lee
Ee Shien Tan
James Soon Chuan Lim
Chia Wei Lim
Rinkoo Dalan
机构
[1] Tan Tock Seng Hospital,Molecular Diagnostic Laboratory
[2] Tan Tock Seng Hospital,Department of Endocrinology
[3] KK Women’s and Children’s Hospital,Department of Paediatrics, Genetics Services
[4] KK Women’s and Children’s Hospital,Biochemical Genetics and National Expanded Newborn Screening, Department of Pathology and Laboratory Medicine
[5] Nanyang Technological University,Lee Kong Chian School of Medicine
[6] National University of Singapore,Yong Loo Lin School of Medicine
来源
BMC Medical Genomics | / 11卷
关键词
Lipid storage myopathy; Multiple acyl-CoA dehydrogenase deficiency; Whole exome sequencing;
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