Unmet Therapeutic Needs of Non-Ambulatory Patients with Duchenne Muscular Dystrophy: A Mixed-Method Analysis

被引：0
|
作者：
Anne L. R. Schuster
Norah L. Crossnohere
Ryan Fischer
Patricia Furlong
John F. P. Bridges
机构：
[1] The Ohio State University College of Medicine,Department of Biomedical Informatics
[2] Parent Project Muscular Dystrophy,Department. of Biomedical Informatics
[3] The Ohio State University College of Medicine,undefined
[4] Lincoln Tower,undefined
来源：
Therapeutic Innovation & Regulatory Science | 2022年 / 56卷
关键词：
Rare diseases; Patient reported outcome measures; Patient-focused drug development;
D O I：
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学科分类号：
摘要：
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页码：572 / 586
页数：14
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