Developing a Gene Therapy Approach for Guanidinoacetate Methyltransferase Deficiency, a Creatine Deficiency Disorder

被引：0
|
作者：
Khoja, Suhail [1 ]
Nitzahn, Matthew [2 ]
Lambert, Jenna [2 ]
Eliav, Adam [2 ]
Nasser, Eram [1 ]
Lipshutz, Gerald S. [1 ]
机构：
[1] Univ Calif Los Angeles, Dept Surg, Los Angeles, CA 90024 USA
[2] Univ Calif Los Angeles, Los Angeles, CA USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
486
引用
收藏
页码：237 / 237
页数：1
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