A Universal Correction Strategy for α-Thalassemia Using CRISPR/AAV-Mediated Genome Editing

被引：0

作者：

Cromer, M. Kyle ^{[1
]}

Wienert, Beeke ^{[2
]}

Hampton, Jessica P. ^{[1
]}

Majeti, Kiran R. ^{[1
]}

Conklin, Bruce R. ^{[2
]}

Porteus, Matthew H. ^{[1
]}

MacKenzie, Tippi C. ^{[3
]}

机构：

[1] Stanford Univ, Pediat, Stanford, CA 94305 USA

[2] Univ Calif San Francisco, Med, San Francisco, CA 94143 USA

[3] Univ Calif San Francisco, Surg, San Francisco, CA 94143 USA

来源：

MOLECULAR THERAPY | 2022年 / 30卷 / 04期

关键词：

D O I：

暂无

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

696

引用

页码：328 / 328

页数：1

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