A Universal Correction Strategy for α-Thalassemia Using CRISPR/AAV-Mediated Genome Editing

被引：0
|
作者：
Cromer, M. Kyle [1 ]
Wienert, Beeke [2 ]
Hampton, Jessica P. [1 ]
Majeti, Kiran R. [1 ]
Conklin, Bruce R. [2 ]
Porteus, Matthew H. [1 ]
MacKenzie, Tippi C. [3 ]
机构：
[1] Stanford Univ, Pediat, Stanford, CA 94305 USA
[2] Univ Calif San Francisco, Med, San Francisco, CA 94143 USA
[3] Univ Calif San Francisco, Surg, San Francisco, CA 94143 USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
696
引用
收藏
页码：328 / 328
页数：1
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