Development of a novel encapsulated non-viral cell-based, BBB-penetrant therapy for MPS I

被引：0
|
作者：
Pearson, Erika [1 ]
Hsu, Anya [1 ]
Tietz, Drew [1 ]
Donovan, Marissa [1 ]
Sohn, Lauren [1 ,2 ]
Hussack, Greg [2 ]
Stanimirovic, Danica
Makino, Elina [1 ]
Ashton-Rickardt, Philip G. [1 ]
机构：
[1] Sigilon Therapeut, Cambridge, MA USA
[2] Natl Res Council Canada, Human Hlth Therapeut Res Ctr, Ottawa, ON, Canada
来源：
MOLECULAR GENETICS AND METABOLISM | 2022年 / 135卷 / 02期
关键词：
D O I：
10.1016/j.ymgme.2021.11.245
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
230
引用
收藏
页码：S94 / S94
页数：1
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