Larotrectinib in TRK fusion-positive pediatric B-cell acute lymphoblastic leukemia

被引:16
|
作者
Schewe, Denis M. [1 ]
Lenk, Lennart [1 ]
Vogiatzi, Fotini [1 ]
Winterberg, Dorothee [1 ]
Rademacher, Annika, V [1 ]
Buchmann, Swantje [1 ]
Henry, Dahlia [2 ]
Bergmann, Anke K. [3 ]
Cario, Gunnar [1 ]
Cox, Michael C. [2 ]
机构
[1] Univ Hosp Schleswig Holstein, Dept Pediat 1, Pediat Hematol Oncol, Arnold Heller Str 3, D-24105 Kiel, Germany
[2] Loxo Oncology Inc, South San Francisco, CA USA
[3] Inst Human Genet, Med Sch Hannover, Hannover, Germany
关键词
D O I
10.1182/bloodadvances.2019000700
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:3499 / +
页数:6
相关论文
共 50 条
  • [41] Economic Evaluation of a Tumour-Agnostic Therapy: Dutch Economic Value of Larotrectinib in TRK Fusion-Positive Cancers
    Michels, Renee E.
    Arteaga, Carlos H.
    Peters, Michel L.
    Kapiteijn, Ellen
    Van Herpen, Carla M. L.
    Krol, Marieke
    APPLIED HEALTH ECONOMICS AND HEALTH POLICY, 2022, 20 (05) : 717 - 729
  • [42] Landscape and outcome of TRK fusion-positive Cancers
    Rosen, Ezra Y.
    Goldman, Debra A.
    Hechtman, Jaclyn F.
    Benayed, Ryma
    Schram, Alison M.
    Cocco, Emiliano
    Shifman, Sophie
    Gong, Yixiao
    Kundra, Ritika
    Solomon, James P.
    Bardelli, Alberto
    Scaltriti, Maurizio
    Drilon, Alexander
    Iasonos, Alexia
    Taylor, Barry S.
    Hyman, David M.
    CLINICAL CANCER RESEARCH, 2020, 26 (12) : 26 - 26
  • [43] Economic Evaluation of a Tumour-Agnostic Therapy: Dutch Economic Value of Larotrectinib in TRK Fusion-Positive Cancers
    Renée E. Michels
    Carlos H. Arteaga
    Michel L. Peters
    Ellen Kapiteijn
    Carla M. L. Van Herpen
    Marieke Krol
    Applied Health Economics and Health Policy, 2022, 20 : 717 - 729
  • [44] EFFICACY AND SAFETY OF LAROTRECTINIB IN ADULT AND PEDIATRIC PATIENTS WITH TROPOMYOSIN RECEPTOR KINASE (TRK) FUSION-POSITIVE PRIMARY CENTRAL NERVOUS SYSTEM (CNS) TUMORS
    Doz, Francois
    van Tilburg, Cornelis M.
    Geoerger, Birgit
    Nysom, Karsten
    Ora, Ingrid
    Boni, Valentina
    Chisholm, Julia
    Chung, Hyun Cheol
    DuBois, Steven G.
    Gallego Melcon, Soledad
    Gerber, Nicolas U.
    Goto, Hiroaki
    Grilley-Olsen, Juneko E.
    Hansford, Jordan R.
    Hong, David S.
    Italiano, Antoine
    Kang, Hyoung Jin
    Capra, Michael
    Schulte, Johannes H.
    Stefanowicz, Joanna
    Tahara, Makoto
    Ziegler, David S.
    Gavrilovic, Igor T.
    Norenberg, Ricarda
    Dima, Laura
    De La Cuesta, Esther
    Laetsch, Theodore W.
    Drilon, Alexander
    Perreault, Sebastien
    NEURO-ONCOLOGY, 2021, 23 : 73 - 74
  • [45] A PEDIATRIC CASE OF A TDT POSITIVE B-CELL ACUTE LYMPHOBLASTIC-LEUKEMIA (B-ALL) WITHOUT BURKITT CHARACTERISTICS
    SHENDE, A
    FESTA, RS
    WEDGWOOD, JF
    LANZKOWSKY, P
    BRITISH JOURNAL OF HAEMATOLOGY, 1988, 70 (01) : 129 - 130
  • [46] Mature B-cell acute lymphoblastic leukemia with t(9;11) translocation: a distinct subset of B-cell acute lymphoblastic leukemia
    Tsao, L
    Draoua, HY
    Osunkwo, I
    Nandula, SV
    Murty, VVS
    Mansukhani, M
    Bhagat, G
    Alobeid, B
    MODERN PATHOLOGY, 2004, 17 (07) : 832 - 839
  • [47] Clinical and Molecular Characteristics of TCF3-Hlf Gene Fusion-Positive B-Cell Precursor Acute Lymphoblastic Leukemia: A Series of 24 Cases from a Large Cohort of Leukemia Patients
    Chen, Xue
    Wang, Fang
    Zhang, Yang
    Ma, Xiaoli
    Yuan, Lili
    Fang, Jiancheng
    Panxiang, Cao
    Chen, Jiaqi
    Zhou, Xiaosu
    Liu, Ming
    Liu, Mingyue
    Liu, Hongxing
    BLOOD, 2021, 138
  • [48] Philadelphia-positive B-Cell acute lymphoblastic leukemia is initiated in an uncommitted progenitor cell
    Pérez-Losada, J
    Gutiérrez-Cianca, N
    Sánchez-García, I
    LEUKEMIA & LYMPHOMA, 2001, 42 (04) : 569 - 576
  • [49] Dysregulation of the DKK1 gene in pediatric B-cell acute lymphoblastic leukemia
    Firtina, Sinem
    Hatirnaz Ng, Ozden
    Erbilgin, Yucel
    Ozbek, Ugur
    Sayitoglu, Muge
    TURKISH JOURNAL OF MEDICAL SCIENCES, 2017, 47 (01) : 357 - 363
  • [50] Blinatumomab-Induced Pneumonitis in a Pediatric Case in B-cell Acute Lymphoblastic Leukemia
    Hizal, Mina
    Yasar, Deniz
    Gursoy, Tugba Ramasli
    Yesil, Sule
    Fettah, Ali
    EUROPEAN RESPIRATORY JOURNAL, 2024, 64