Gene therapy for RPE65-mediated inherited retinal dystrophy completes phase 3

被引：7
作者：
Lee, Helena [1 ]
Lotery, Andrew [1 ]
机构：
[1] Univ Southampton, Fac Med, Clin & Expt Sci, Southampton SO16 6YD, Hants, England
来源：
LANCET | 2017年 / 390卷 / 10097期
基金：
英国医学研究理事会;
关键词：
LEBERS CONGENITAL AMAUROSIS; ADENOASSOCIATED VIRUS; RPE65; MUTATIONS; SAFETY; TRIAL;
D O I：
10.1016/S0140-6736(17)31622-7
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：823 / 824
页数：2
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