Gene Therapy with Adeno-associated Virus for Cystic Fibrosis

被引：0

作者：

Karda, Rajvinder ^{[1
]}

Buckley, Suzanne M. K. ^{[2
]}

Waddington, Simon N. ^{[2
,3
]}

机构：

[1] Univ London Imperial Coll Sci Technol & Med, Dept Surg & Canc, London, England

[2] UCL, Gene Transfer Technol Grp, London, England

[3] Univ Witwatersrand, Wits SAMRC Antiviral Gene Therapy Res Unit, Johannesburg, South Africa

来源：

AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE | 2016年 / 193卷 / 03期

关键词：

LONG-TERM SAFETY; PHASE 2B TRIAL; IN-VITRO; VECTOR; EXPRESSION; VIVO; CFTR; TRANSDUCTION; CORRECTS; EFFICACY;

D O I：

暂无

中图分类号：

R4 [临床医学];

学科分类号：

1002 ; 100602 ;

摘要：

引用

页码：234 / 236

页数：3

共 22 条

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