Lentiviral-Mediated Gene Therapy Restores B Cell Homeostasis and Tolerance in Wiskott-Aldrich Syndrome Patients

被引：0

作者：

Castiello, Maria Carmina ^{[1
]}

Pala, Francesca ^{[1
]}

Morbach, Henner ^{[2
]}

Schickel, Jean-Nicolas ^{[2
]}

Scaramuzza, Samantha ^{[1
]}

Chamberlain, Nicolas ^{[2
]}

Romberg, Neil ^{[3
]}

Ferrua, Francesca ^{[1
,4
,5
]}

Candotti, Fabio ^{[6
]}

van der Burg, Mirjam ^{[7
]}

Naldini, Luigi ^{[1
,5
]}

Aiuti, Alessandro ^{[1
,4
,5
]}

Meffre, Eric ^{[2
]}

Bosticardo, Marita ^{[1
]}

Villa, Anna ^{[1
,8
]}

机构：

[1] IRCCS San Raffaele Sci Inst, San Raffaele Telethon Inst Gene Therapy SR TIGET, Milan, Italy

[2] Yale Univ, Sch Med, Dept Immunobiol, New Haven, CT USA

[3] Yale Univ, Sch Med, Dept Pediat, Div Allergy & Clin Immunol, New Haven, CT 06510 USA

[4] IRCCS San Raffaele Sci Inst, Pediat Immunohematol & Bone Marrow Transplantat U, Milan, Italy

[5] Univ Vita Salute San Raffaele, Milan, Italy

[6] NHGRI, Genet & Mol Biol Branch, Bethesda, MD 20892 USA

[7] Univ Med Ctr Rotterdam, Erasmus MC, Dept Immunol, Rotterdam, Netherlands

[8] IRGB CNR, Milan Unit, Milan, Italy

来源：

关键词：

D O I：

10.1016/S1525-0016(16)33089-1

中图分类号：

Q81 [生物工程学（生物技术）]; Q93 [微生物学];

学科分类号：

071005 ; 0836 ; 090102 ; 100705 ;

摘要：

280

引用

页码：S112 / S112

页数：1