Manufacture of an ATMP for the treatment of X-linked Severe Combined Immunodeficiency (X-SCID)

被引：0
作者：
Leon-Rico, D. [1 ,2 ]
Schott, J. W. [1 ,5 ]
Armenteros-Monterroso, E. [1 ,2 ]
Buckland, K. F. [1 ,2 ]
Diasakou, A. [1 ,2 ]
Pereira, I. [1 ,2 ]
Ferreira, C. B. [1 ]
Cavazza, A. [1 ]
Shaw, K. L. [3 ]
Armant, M. [4 ]
Kohn, D. B. [3 ]
Pai, S. Y. [4 ]
Thasher, A. J. [1 ,2 ]
Booth, C. [1 ,2 ]
机构：
[1] UCL GOS Inst Child Hlth, London, England
[2] Great Ormond St Hosp Children NHS Fdn Trust, London, England
[3] Univ Calif Los Angeles, Los Angeles, CA 90024 USA
[4] Boston Childrens Hosp, Boston, MA USA
[5] Hannover Med Sch, Hannover, Germany
来源：
HUMAN GENE THERAPY | 2019年 / 30卷 / 11期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
P226
引用
收藏
页码：A86 / A86
页数：1
相关论文
共 50 条
  • [41] A NOVEL X-LINKED COMBINED IMMUNODEFICIENCY
    BROOKS, EG
    SCHMALSTIEG, FC
    WIRT, DP
    ROSENBLATT, H
    ADKINS, LT
    RUDLOFF, HE
    GOLDMAN, AS
    PEDIATRIC RESEARCH, 1990, 27 (04) : A154 - A154
  • [42] A NOVEL X-LINKED COMBINED IMMUNODEFICIENCY
    BROOKS, EG
    SCHMALSTIEG, FC
    WIRT, DP
    ROSENBLATT, H
    ADKINS, LT
    GOLDMAN, AS
    CLINICAL RESEARCH, 1990, 38 (01): : A53 - A53
  • [43] Development of effective and safe lentiviral vectors for the treatment of X-linked severe combined immunodeficiency
    Zhou, Sheng
    Greene, Michael
    Lu, Taihe
    Shou, Yan
    Sorrentino, Brian P.
    BLOOD CELLS MOLECULES AND DISEASES, 2008, 40 (02) : 285 - 285
  • [44] GENETIC SYNTENY OF PROXIMAL XQ REGIONS, INCLUDING X-LINKED SEVERE COMBINED IMMUNODEFICIENCY (SCID), IN DOG AND MAN
    DESCHENES, SM
    PUCK, JM
    DUTRA, A
    SOMBERG, RL
    FELSBURG, PJ
    HENTHORN, PS
    AMERICAN JOURNAL OF HUMAN GENETICS, 1993, 53 (03) : 992 - 992
  • [45] Treatment of X-linked severe combined immunodeficiency by in utero transplantation of paternal bone marrow
    Flake, AW
    Roncarolo, MG
    Puck, JM
    AlmeidaPorada, G
    Evans, MI
    Johnson, MP
    Abella, EM
    Harrison, DD
    Zanjani, ED
    NEW ENGLAND JOURNAL OF MEDICINE, 1996, 335 (24) : 1806 - 1810
  • [46] GENETIC-ANALYSIS OF CANINE X-LINKED SEVERE COMBINED IMMUNODEFICIENCY
    HENTHORN, PS
    DESCHENES, SM
    DUTRA, AS
    JACKSON, GM
    SOMBERG, RL
    FELSBURG, PJ
    PUCK, JM
    JOURNAL OF CELLULAR BIOCHEMISTRY, 1994, : 206 - 206
  • [47] Cell function in canine X-linked severe combined immunodeficiency (XSCID).
    Hartnett, BJ
    Somberg, RL
    Krakowka, S
    Ochs, HD
    Felsburg, PJ
    FASEB JOURNAL, 1998, 12 (05) : A921 - A921
  • [48] HISTOLOGIC CHARACTERIZATION OF THE THYMUS IN CANINE X-LINKED SEVERE COMBINED IMMUNODEFICIENCY
    SNYDER, PW
    KAZACOS, EA
    FELSBURG, PJ
    CLINICAL IMMUNOLOGY AND IMMUNOPATHOLOGY, 1993, 67 (01): : 55 - 67
  • [49] X-linked severe combined immunodeficiency in a family of Cardigan Welsh corgis
    Pullen, RP
    Somberg, RL
    Felsburg, PJ
    Henthorn, PS
    JOURNAL OF THE AMERICAN ANIMAL HOSPITAL ASSOCIATION, 1997, 33 (06) : 494 - 499
  • [50] ACUTE MONOCYTIC LEUKEMIA IN A DOG WITH X-LINKED SEVERE COMBINED IMMUNODEFICIENCY
    FELSBURG, PJ
    SOMBERG, RL
    KRAKOWKA, GS
    CLINICAL AND DIAGNOSTIC LABORATORY IMMUNOLOGY, 1994, 1 (04) : 379 - 384
12345