Resolution of Serious Vaso-occlusive Pain Crises: Results From The Ongoing Phase 1/2 HGB-206 Group C Study of Lentiglobin for Sickle Cell Disease (SCD) Gene Therapy

被引：0

作者：

Mapara, Markus ^{[1
]}

Walters, Mark ^{[2
]}

Thompson, Alexis ^{[3
,4
]}

Kwiatkowski, Janet ^{[5
,6
]}

Krishnamurti, Lakshmanan ^{[7
]}

Aygun, Banu ^{[8
]}

Kasow, Kimberly ^{[9
]}

Rifkin-Zenenberg, Stacey ^{[10
]}

Schmidt, Manfred ^{[11
]}

Nnamani, Mauris ^{[12
]}

VanNest, Sara ^{[12
]}

Pierciey, Francis, Jr. ^{[12
]}

Miller, Alex ^{[12
]}

Chen, Ren ^{[12
]}

Kim, Dennis ^{[12
]}

Goyal, Sunita ^{[12
]}

Kanter, Julie ^{[13
]}

Tisdale, John ^{[14
]}

机构：

[1] Columbia Univ, Med Ctr, New York, NY USA

[2] UCSF Benioff Childrens Hosp Oakland, Oakland, CA USA

[3] Northwestern Univ, Feinberg Sch Med, Chicago, IL 60611 USA

[4] Ann & Robert H Lurie Childrens Hosp Chicago, Chicago, IL USA

[5] Childrens Hosp Philadelphia, Philadelphia, PA 19104 USA

[6] Univ Penn, Perelman Sch Med, Philadelphia, PA 19104 USA

[7] Emory Univ, Childrens Healthcare Atlanta, Atlanta, GA 30322 USA

[8] Cohen Childrens Med Ctr, Queens, NY USA

[9] Univ N Carolina, Chapel Hill, NC 27515 USA

[10] Hackensack Univ, Med Ctr, Hackensack, NJ USA

[11] GeneWerk GmbH, Heidelberg, Germany

[12] Bluebird Bio Inc, Cambridge, MA USA

[13] Univ Alabama Birmingham, Birmingham, AL USA

[14] NIH, Bldg 10, Bethesda, MD 20892 USA

来源：

BONE MARROW TRANSPLANTATION | 2021年 / 56卷 / SUPPL 1期

关键词：

D O I：

暂无

中图分类号：

Q6 [生物物理学];

学科分类号：

071011 ;

摘要：

O056

引用

页码：66 / 68

页数：3

共 42 条

[1] Resolution of Serious Vaso-Occlusive Pain Crises and Reduction in Patient-Reported Pain Intensity: Results from the Ongoing Phase 1/2 HGB-206 Group C Study of LentiGlobin for Sickle Cell Disease (bb1111) Gene Therapy
Thompson, Alexis A.
Walters, Mark C.
Mapara, Markus Y.
Kwiatkowski, Janet L.
Krishnamurti, Lakshmanan
Aygun, Banu
Kasow, Kimberly A.
Rifkin-Zenenberg, Stacey
Schmidt, Manfred
DelCarpini, Jay
Pierciey, Francis J., Jr.
Miller, Alexandra L.
Gallagher, Meghan E.
Chen, Ren
Goyal, Sunita
Kanter, Julie
Tisdale, John F.
BLOOD, 2020, 136
[2] Lentiglobin for Sickle Cell Disease (SCD) Gene Therapy (GT): Updated Results in Group C Patients from the Phase 1/2 Hgb-206 Study
Walters, Mark C.
Kanter, Julie
Kwiatkowski, Janet L.
Krishnamurti, Lakshmanan
Mapara, Markus Y.
Schmidt, Manfred
Miller, Alexandra L.
Pierciey, Jr. Francis J.
Bonner, Melissa
Huang, Wenmei
Ribeil, Jean-Antoine
Thompson, Alexis A.
Tisdale, John F.
BIOLOGY OF BLOOD AND MARROW TRANSPLANTATION, 2020, 26 (03) : S1 - S2
[3] Resolution of Sickle Cell Disease (SCD) Manifestations in Patients Treated with Lentiglobin Gene Therapy: Updated Results from the Phase 1/2 HGB-206 Group C Study
Tisdale, John F.
Kanter, Julie
Mapara, Markus Y.
Kwiatkowski, Janet L.
Krishnamurti, Lakshmanan
Schmidt, Manfred
Miller, Alexandra L.
Pierciey, Francis J., Jr.
Huang, Wenmei
Ribeil, Jean-Antoine
Thompson, Alexis A.
Walters, Mark C.
MOLECULAR THERAPY, 2020, 28 (04) : 553 - 553
[4] Lentiglobin for Sickle Cell Disease (SCD) Gene Therapy (GT): Updated Results in Group C Patients from the Phase 1/2 HGB-206 Study
Mapara, Markus Y.
Tisdale, John F.
Kanter, Julie
Kwiatkowski, Janet L.
Krishnamurti, Lakshmanan
Schmidt, Manfred
Miller, Alexandra L.
Pierciey, Francis J., Jr.
Bonner, Melissa
Huang, Wenmei
Ribeil, Jean-Antoine
Thompson, Alexis A.
Walters, Mark C.
BONE MARROW TRANSPLANTATION, 2020, 55 (SUPPL 1) : 78 - 79
[5] UPDATED RESULTS FROM THE HGB-206 GROUP C STUDY OF LENTIGLOBIN FOR SICKLE CELL DISEASE GENE THERAPY
Kwiatkowski, Janet
Thompson, Alexis
Walters, Mark
Mapara, Markus
Krishnamurti, Lakshmanan
Aygun, Banu
Kasow, Kimberly
Rifkin-Zenenberg, Stacey
Schmidt, Manfred
Miller, Alex
Gallagher, Meghan
Chen, Ren
Kim, Dennis
Goyal, Sunita
Kanter, Julie
Tisdale, John
PEDIATRIC BLOOD & CANCER, 2021, 68 : S2 - S3
[6] Resolution of Sickle Cell Disease Manifestations in Patients Treated with Lentiglobin Gene Therapy: Updated Results from the Phase 1/2 Hgb-206 Group C Study
Kanter, Julie
Tisdale, John F.
Mapara, Markus Y.
Kwiatkowski, Janet L.
Krishnamurti, Lakshmanan
Schmidt, Manfred
Miller, Alexandra L.
Pierciey, Francis J., Jr.
Huang, Wenmei
Ribeil, Jean-Antoine
Thompson, Alexis A.
Walters, Mark C.
BLOOD, 2019, 134
[7] Resolution of sickle cell disease manifestations in patients treated with LentiGlobin gene therapy: updated results from the phase 1/2 HGB-206 Group C study
Asmal, M.
Kanter, J.
Tisdale, J. F.
Mapara, M. Y.
Kwiatkowski, J. L.
Krishnamurti, L.
Schmidt, M.
Miller, A. L.
Pierciey, F. J., Jr.
Huang, W.
Ribeil, J. -A.
Thompson, A. A.
Walters, M. C.
BRITISH JOURNAL OF HAEMATOLOGY, 2020, 189 : 33 - 33
[8] LENTIGLOBIN GENE THERAPY FOR PATIENTS WITH SICKLE CELL DISEASE: UPDATED RESULTS FROM STUDY HGB-206
Thompson, Alexis
Krishnamurti, Lakshmanan
Mapara, Markus
Kwiatkowski, Janet
Tisdale, John
Schmidt, Manfred
Miller, Alexandra
Pierciey, Francis, Jr.
Huang, Wenmei
Ribeil, Jean-Antoine
Kanter, Julie
Walters, Mark
PEDIATRIC BLOOD & CANCER, 2020, 67 : S32 - S32
[9] LentiGlobin Gene Therapy in Patients with Sickle Cell Disease: Updated Interim Results from HGB-206
Tisdale, John F.
Kanter, Julie
Mapara, Markus Y.
Kwiatkowski, Janet L.
Krishnamurti, Lakshmanan
Schmidt, Manfred
Miller, Alexandra L.
Pierciey, Francis J.
Shi, Weiliang
Ribeil, Jean-Antoine
Asmal, Mohammed
Thompson, Alexis A.
Walters, Mark C.
MOLECULAR THERAPY, 2019, 27 (04) : 1 - 1
[10] Lentiglobin gene therapy in patients with sickle cell disease: Updated interim results from HGB-206
Mapara, Markus Y.
Tisdale, John F.
Kanter, Julie
Kwiatkowski, Janet L.
Krishnamurti, Lakshmanan
Schmidt, Manfred
Miller, Alexandra L.
Pierciey, Francis J., Jr.
Shi, Weiliang
Ribeil, Jean-Antoine
Asmal, Mohammed
Thompson, Alexis A.
Walters, Mark
BONE MARROW TRANSPLANTATION, 2019, 54 : 77 - 78

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