Single Vector AAV Approach to Genome Editing in Pompe Disease

被引：0
|
作者：
Arnson, Benjamin [1 ]
Wang, Jason [2 ]
Courtney, David [3 ]
Han, Sang-oh [1 ]
Li, Songtao [1 ]
Cullen, Bryan R. [3 ]
Bursac, Nenad [2 ]
Koeberl, Dwight [1 ]
机构：
[1] Duke Univ, Pediat Med Genet, Durham, NC USA
[2] Duke Univ, Biomed Engn, Durham, NC USA
[3] Duke Univ, Mol Genet & Microbiol, Durham, NC USA
来源：
MOLECULAR THERAPY | 2021年 / 29卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
600
引用
收藏
页码：291 / 291
页数：1
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