ACTIVATE: A phase 3, randomized, multicenter, double-blind, placebo-controlled study of mitapivat in adults with Pyruvate kinase deficiency who are not regularly transfused

被引：0

作者：

Al-Samkari, H. ^{[1
]}

Galacteros, F. ^{[2
]}

Glenthoj, A. ^{[3
]}

Rothman, J. A. ^{[4
]}

Andres, O. ^{[5
]}

Grace, R. F. ^{[6
]}

Arias, Morado M. ^{[7
]}

Layton, D. M. ^{[8
]}

Onodera, K. ^{[9
]}

Verhovsek, M. ^{[10
]}

Barcellini, W. ^{[11
]}

Judge, M. P. ^{[12
]}

Beynon, V ^{[12
]}

Xu, E. ^{[12
]}

Hawkins, P. ^{[12
]}

Zagadailov, E. ^{[12
]}

Gheuens, S. ^{[12
]}

van Beers, E. J. ^{[13
]}

机构：

[1] Harvard Med Sch, Massachusetts Gen Hosp, Div Hematol, Boston, MA 02115 USA

[2] CHU Henri Mondor, Unite Malad Genet Globule Rouge, Creteil, France

[3] Rigshosp, Dept Hematol, Copenhagen, Denmark

[4] Duke Univ, Med Ctr, Durham, NC USA

[5] Univ Wurzburg, Dept Paediat, Wurzburg, Germany

[6] Dana Farber Boston Childrens Canc & Blood Disorde, Boston, MA USA

[7] Hosp Univ La Paz, Hematol Dept, Madrid, Spain

[8] Hammersmith Hosp, Imperial Coll Healthcare NHS Trust, London, England

[9] Tohoku Univ Hosp, Sendai, Miyagi, Japan

[10] McMaster Univ, Hamilton, ON, Canada

[11] Fdn IRCCS CaGranda Osped Maggiore Policlin, Milan, Italy

[12] Agios Pharmaceut Inc, Cambridge, MA USA

[13] Univ Utrecht, Univ Med Ctr Utrecht, Dept Internal Med, Van Creveldklin, Utrecht, Netherlands

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D O I：

暂无

中图分类号：

R73 [肿瘤学];

学科分类号：

100214 ;

摘要：

V215

引用

页码：40 / 40

页数：1