[1] Harvard Med Sch, Ocular Genom Inst, Dept Opthamol, Boston, MA 02115 USA
[2] Schepens Eye Res Inst, Grousbeck Gene Therapy Ctr, Boston, MA USA
[3] Broad Inst MIT & Harvard, Cambridge, MA 02142 USA
[4] Harvard Univ, Harvard Stem Cell Inst, Cambridge, MA 02138 USA