Risk factors and outcomes according to age at transplantation with an HLA-identical sibling for sickle cell disease

被引：48

作者：

Cappelli, Barbara ^{[1
,2
]}

Volt, Fernanda ^{[1
,2
,3
]}

Tozatto-Maio, Karina ^{[1
,2
]}

Maria Scigliuolo, Graziana ^{[4
]}

Ferster, Alina ^{[5
]}

Dupont, Sophie ^{[3
]}

Simoes, Belinda Pinto ^{[6
]}

Al-Seraihy, Amal ^{[7
]}

Aljurf, Mahmoud D. ^{[7
]}

Almohareb, Fahad ^{[8
]}

Belendez, Cristina ^{[8
]}

Matthes, Susanne ^{[9
]}

Dhedin, Nathalie ^{[10
]}

Pondarre, Corinne ^{[11
]}

Dalle, Jean-Hugues ^{[12
,13
]}

Bertrand, Yves ^{[14
]}

Vannier, Jean Pierre ^{[15
]}

Kuentz, Mathieu ^{[11
]}

Lutz, Patrick ^{[16
]}

Michel, Gerard ^{[17
,18
,19
]}

Rafii, Hanadi ^{[1
,2
]}

Neven, Benedicte ^{[20
]}

Zecca, Marco ^{[21
]}

Bader, Peter ^{[22
]}

Cavazzana, Marina ^{[23
,24
]}

Labopin, Myriam ^{[25
]}

Locatelli, Franco ^{[26
]}

Magnani, Alessandra ^{[23
]}

Ruggeri, Annalisa ^{[1
,2
,3
]}

Rocha, Vanderson ^{[27
]}

Bernaudin, Francoise ^{[11
]}

de la Fuente, Josu ^{[28
]}

Corbacioglu, Selim ^{[29
]}

Gluckman, Eliane ^{[1
,2
]}

机构：

[1] Ctr Sci Monaco, Monte Carlo, Monaco

[2] Univ Paris Diderot, Hop St Louis, Eurocord, Paris, France

[3] Univ Sao Paulo, Fac Med Ribeirao Preto, Ribeirao Preto, Brazil

[4] Univ Libre Bruxelles, Hosp Univ Enfants Reine Fabiola, Hematooncol Unit, Brussels, Belgium

[5] Clin Univ St Luc, Hematooncol Unit, Brussels, Belgium

[6] King Faisal Specialist Hosp & Res Ctr, Paediat SCT Program, Riyadh, Saudi Arabia

[7] King Faisal Specialist Hosp & Res Ctr, Hematol HSCT Program, Riyadh, Saudi Arabia

[8] Hosp Univ Materno Infantil Gregorio Maranon, Oncohematol Pediatr, Madrid, Spain

[9] Med Univ Vienna, St Anna Childrens Hosp, Stem Cell Transplantat Unit, Vienna, Austria

[10] Hosp St Louis, Adolescent & Young Adults Hematol Dept, Paris, France

[11] Paris XII Univ, Ctr Hosp Intercommunal Creteil, Referral Ctr Sickle Cell Dis, Dept Pediat,INSERM,U955, Creteil, France

[12] Hosp Robert Debre, Hematoimmunol Dept, Paris, France

[13] Paris 7 Paris Diderot Univ, Paris, France

[14] Univ Hosp Lyon, Dept Pediat Hematol & Oncol, Lyon, France

[15] Inst Rech & Innovat Biomed, PANTHER Physiopathol Autoimmunite Malad Neuromusl, Unite Mixte Rech U 1234, Fac Med Pharm, Rouen, France

[16] CHU Strasbourg, Serv Hemato Oncol Pediat, Strasbourg, France

[17] Aix Marseille Univ, Dept Pediat Hematol & Oncol, Marseille, France

[18] Aix Marseille Univ, Res Unit Equipe Accueil 3279, Marseille, France

[19] Timone Childrens Hosp Marseille, Marseille, France

[20] Necker Childrens Hosp, AP HP, Pediat Hematol Immunol Dept, Paris, France

[21] Fdn IRCCS Policlin San Matteo, Pediat Hematol Oncol Unit, Pavia, Italy

[22] Univ Hosp, Clin Children & Adolescents, Dept Stem Cell Transplantat & Immunol, Frankfurt, Germany

[23] Necker Enfants Malades Univ Hosp, AP HP, Dept Biotherapy, Paris, France

[24] Groupe Hosp Univ Ouest, AP HP, Biotherapy Clin Invest Ctr, Paris, France

[25] Hop St Antoine, AP HP, Serv Hematol Clin & Therapie Cellulaire, F-75012 Paris, France

[26] Sapienza Univ Rome, Bambino Gesu Children Hosp, Dept Hematopoiet Stem Cell Transplantat, Rome, Italy

[27] Univ Sao Paulo, Fac Med, Serv Hematol Hemoterapia & Terapia Celular, Sao Paulo, SP, Brazil

[28] Imperial Coll, St Marys Hosp, Dept Pediat, London, England

[29] Univ Regensburg, Dept Pediat Hematol Oncol & Stem Cell Transplanta, Regensburg, Germany

来源：

HAEMATOLOGICA | 2019年 / 104卷 / 12期

关键词：

THALASSEMIA; CHILDREN; ADULTS;

D O I：

10.3324/haematol.2019.216788

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：E543 / E546

页数：4

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