Two Phase 2 Trials to Assess Production of Dystrophin in Patients with Nonsense Mutation Duchenne Muscular Dystrophy Receiving Ataluren

被引：0
|
作者：
Nelson, S.
Penematsa, V
Chou, C.
Trifillis, P.
Bibbiani, F.
McIntosh, J.
机构：
来源：
ANNALS OF NEUROLOGY | 2019年 / 86卷
关键词：
Neuromuscular Disorders; Rare Diseases;
D O I：
暂无
中图分类号：
R74 [神经病学与精神病学];
学科分类号：
摘要：
186
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收藏
页码：S127 / S127
页数：1
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