Chronic ivacaftor treatment: Getting F508del-CFTR into more trouble?

被引：7
作者：
Mall, Marcus A. [1 ,2 ,3 ]
Sheppard, David N. [4 ]
机构：
[1] Heidelberg Univ, Translat Lung Res Ctr Heidelberg TLRC, Dept Translat Pulmonol, D-69120 Heidelberg, Germany
[2] Heidelberg Univ, Div Pediat Pulmonol, D-69120 Heidelberg, Germany
[3] Heidelberg Univ, Cyst Fibrosis Ctr, D-69120 Heidelberg, Germany
[4] Univ Bristol, Sch Physiol & Pharmacol, Bristol BS8 1TD, Avon, England
来源：
JOURNAL OF CYSTIC FIBROSIS | 2014年 / 13卷 / 06期
关键词：
CYSTIC-FIBROSIS; CFTR POTENTIATOR; IN-VITRO; MUTATION; THERAPY; MODELS;
D O I：
10.1016/j.jcf.2014.10.001
中图分类号：
R56 [呼吸系及胸部疾病];
学科分类号：
摘要：
引用
收藏
页码：605 / 607
页数：3
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