Systemic Antisense-Mediated Exon Skipping in Mouse Models for Duchenne Muscular Dystrophy

被引:0
|
作者
Aartsma-Rus, Annemieke [1 ]
Heemskerk, Hans [1 ]
De Winter, Christa [1 ]
Van Putten, Maaike [1 ]
Janson, Anneke [2 ]
Verschuuren, Jan [1 ]
Den Dunnen, Johan [1 ]
Van Deutekom, Judith [2 ]
Van Ommen, Gert-Jan [1 ]
机构
[1] Leiden Univ, Med Ctr, Leiden, Netherlands
[2] Prosensa Therapeut, Leiden, Netherlands
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D O I
暂无
中图分类号
Q81 [生物工程学(生物技术)]; Q93 [微生物学];
学科分类号
071005 ; 0836 ; 090102 ; 100705 ;
摘要
425
引用
收藏
页码:S166 / S166
页数:1
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