Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia (vol 21, pg 3548, 2017)

被引:22
作者
An, Ding
Schneller, Jessica L.
Frassetto, Andrea
Liang, Shi
Zhu, Xuling
Park, Ji-Sun
Theisen, Matt
Hong, Sue-Jean
Zhou, Jenny
Rajendran, Raj
Levy, Becca
Howell, Rebecca
Besin, Gilles
Presnyak, Vladimir
Sabnis, Staci
Murphy-Benenato, Kerry E.
Kumarasinghe, E. Sathyajith
Salerno, Timothy
Mihai, Cosmin
Lukacs, Christine M.
Chandler, Randy J.
Guey, Lin T.
Venditti, Charles P.
Martini, Paolo G. V.
机构
来源
CELL REPORTS | 2018年 / 24卷 / 09期
关键词
D O I
10.1016/j.celrep.2018.08.049
中图分类号
Q2 [细胞生物学];
学科分类号
071009 ; 090102 ;
摘要
引用
收藏
页码:2520 / 2520
页数:1
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  • [1] Systemic Messenger RNA Therapy as a Treatment for Methylmalonic Acidemia
    An, Ding
    Schneller, Jessica L.
    Frassetto, Andrea
    Liang, Shi
    Zhu, Xuling
    Park, Ji-Sun
    Theisen, Matt
    Hong, Sue-Jean
    Zhou, Jenny
    Rajendran, Raj
    Levy, Becca
    Howell, Rebecca
    Besin, Gilles
    Presnyak, Vladimir
    Sabnis, Staci
    Murphy-Benenato, Kerry E.
    Kumarasinghe, E. Sathyajith
    Salerno, Timothy
    Mihai, Cosmin
    Lukacs, Christine M.
    Chandler, Randy J.
    Guey, Lin T.
    Venditti, Charles P.
    Martini, Paolo G. V.
    [J]. CELL REPORTS, 2017, 21 (12): : 3548 - 3558