Long-Term Efficacy and Safety of the Microsomal Triglyceride Transfer Protein Inhibitor Lomitapide in Patients With Homozygous Familial Hypercholesterolemia

被引:103
作者
Blom, Dirk J. [1 ]
Averna, Maurizio R. [2 ]
Meagher, Emma A. [3 ]
Theron, Hendrik du Toit [4 ]
Sirtori, Cesare R.
Hegele, Robert A. [5 ,6 ]
Shah, Prediman K. [7 ]
Gaudet, Daniel [8 ]
Stefanutti, Claudia [9 ]
Vigna, Giovanni B. [10 ]
Larrey, Dominique [11 ]
Bloedon, LeAnne T. [12 ]
Foulds, Pamela [12 ]
Rader, Daniel J. [3 ]
Cuchel, Marina [3 ]
机构
[1] Univ Cape Town, Cape Town, South Africa
[2] Univ Palermo, Palermo, Italy
[3] Univ Penn, Philadelphia, PA 19104 USA
[4] Netcare Private Hosp, Bloemfontein, South Africa
[5] Osped Niguarda Ca Granda, Milan, Italy
[6] Univ Western Ontario, London, ON, Canada
[7] Cedars Sinai Heart Inst, Los Angeles, CA USA
[8] Univ Montreal, Chicoutimi, PQ, Canada
[9] Univ Roma Sapienza, Rome, Italy
[10] Univ Ferrara, Ferrara, Italy
[11] CHRU Montpellier, Montpellier, France
[12] Aeger Pharmaceut, Cambridge, MA USA
关键词
lomitapide;
D O I
10.1161/CIRCULATIONAHA.117.028208
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
引用
收藏
页码:332 / 335
页数:4
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