Evolution of haemophilia integrated care in the era of gene therapy: Treatment centre's readiness in United States and EU

被引：15

作者：

Miesbach, Wolfgang ^{[1
]}

Pasi, K. John ^{[2
]}

Pipe, Steven W. ^{[3
,4
]}

Hermans, Cedric ^{[5
]}

O'Mahony, Brian ^{[6
,7
]}

Guelcher, Christine ^{[8
]}

Steiner, Bruno ^{[9
]}

Skinner, Mark W. ^{[10
,11
]}

机构：

[1] Univ Hosp Frankfurt, Frankfurt, Germany

[2] Barts & London Queen Marys Sch Med & Dent, Royal London Haemophilia Ctr, London, England

[3] Univ Michigan, Ann Arbor, MI 48109 USA

[4] Natl Hemophilia Fdn, New York, NY USA

[5] Univ Catholique Louvain UCLouvain, Clin Univ St Luc, Brussels, Belgium

[6] Trinity Coll Dublin, Dublin, Ireland

[7] Irish Haemophilia Soc, Dublin, Ireland

[8] Childrens Natl Hosp, Washington, DC USA

[9] Bloodworks Northwest, Washington Ctr Bleeding Disorders, Seattle, WA USA

[10] Inst Policy Adv Ltd, Washington, DC USA

[11] McMaster Univ, Hamilton, ON, Canada

来源：

HAEMOPHILIA | 2021年 / 27卷 / 04期

关键词：

gene therapy; haemophilia care; haemophilia treatment; treatment centres; MODELS;

D O I：

10.1111/hae.14309

中图分类号：

R5 [内科学];

学科分类号：

1002 ; 100201 ;

摘要：

引用

页码：511 / 514

页数：4

共 13 条

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