Evolution of haemophilia integrated care in the era of gene therapy: Treatment centre's readiness in United States and EU

被引：12
作者：
Miesbach, Wolfgang [1 ]
Pasi, K. John [2 ]
Pipe, Steven W. [3 ,4 ]
Hermans, Cedric [5 ]
O'Mahony, Brian [6 ,7 ]
Guelcher, Christine [8 ]
Steiner, Bruno [9 ]
Skinner, Mark W. [10 ,11 ]
机构：
[1] Univ Hosp Frankfurt, Frankfurt, Germany
[2] Barts & London Queen Marys Sch Med & Dent, Royal London Haemophilia Ctr, London, England
[3] Univ Michigan, Ann Arbor, MI 48109 USA
[4] Natl Hemophilia Fdn, New York, NY USA
[5] Univ Catholique Louvain UCLouvain, Clin Univ St Luc, Brussels, Belgium
[6] Trinity Coll Dublin, Dublin, Ireland
[7] Irish Haemophilia Soc, Dublin, Ireland
[8] Childrens Natl Hosp, Washington, DC USA
[9] Bloodworks Northwest, Washington Ctr Bleeding Disorders, Seattle, WA USA
[10] Inst Policy Adv Ltd, Washington, DC USA
[11] McMaster Univ, Hamilton, ON, Canada
来源：
HAEMOPHILIA | 2021年 / 27卷 / 04期
关键词：
gene therapy; haemophilia care; haemophilia treatment; treatment centres; MODELS;
D O I：
10.1111/hae.14309
中图分类号：
R5 [内科学];
学科分类号：
1002 ; 100201 ;
摘要：
引用
收藏
页码：511 / 514
页数：4
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