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Adverum Biotechnologies, 2020, ADVERUM BIOTECHNOLOG
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T-tubule disorganization and defective excitation-contraction coupling in muscle fibers lacking myotubularin lipid phosphatase
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Al-Qusairi, Lama
;
Weiss, Norbert
;
Toussaint, Anne
;
Berbey, Celine
;
Messaddeq, Nadia
;
Kretz, Christine
;
Sanoudou, Despina
;
Beggs, Alan H.
;
Allard, Bruno
;
Mandel, Jean-Louis
;
Laporte, Jocelyn
;
Jacquemond, Vincent
;
Buj-Bello, Anna
.
PROCEEDINGS OF THE NATIONAL ACADEMY OF SCIENCES OF THE UNITED STATES OF AMERICA,
2009, 106 (44)
:18763-18768

Al-Qusairi, Lama
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Weiss, Norbert
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Lyon 1, Unite Mixte Rech 5123, F-69622 Villeurbanne, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Toussaint, Anne
论文数: 0 引用数: 0
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机构:
Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Berbey, Celine
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Lyon 1, Unite Mixte Rech 5123, F-69622 Villeurbanne, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Messaddeq, Nadia
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Imaging Ctr Electron Micros, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Kretz, Christine
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Sanoudou, Despina
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Childrens Hosp Boston, Manton Ctr Orphan Dis Res,Genet Div, Boston, MA 02115 USA
Harvard Univ, Sch Med, Childrens Hosp Boston, Manton Ctr Orphan Dis Res,Program Genom, Boston, MA 02115 USA Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Beggs, Alan H.
论文数: 0 引用数: 0
h-index: 0
机构:
Harvard Univ, Sch Med, Childrens Hosp Boston, Manton Ctr Orphan Dis Res,Genet Div, Boston, MA 02115 USA
Harvard Univ, Sch Med, Childrens Hosp Boston, Manton Ctr Orphan Dis Res,Program Genom, Boston, MA 02115 USA Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Allard, Bruno
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Lyon 1, Unite Mixte Rech 5123, F-69622 Villeurbanne, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Mandel, Jean-Louis
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

Laporte, Jocelyn
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France

论文数: 引用数:
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Buj-Bello, Anna
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France Univ Strasbourg 1, Coll France, Unite Mixte Rech 7104,Dept Neurobiol & Genet, CNRS,INSRM,U964,Inst Genet & Biol Mol & Cellulair, F-67404 Illkirch Graffenstaden, France
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Al-Zaidy, Samiah
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Pickard, A. Simon
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Kotha, Kavitha
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Alfano, Lindsay N.
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Lowes, Linda
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Paul, Grace
;
Church, Kathleen
;
Lehman, Kelly
;
Sproule, Douglas M.
;
Dabbous, Omar
;
Maru, Benit
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Berry, Katherine
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Arnold, W. David
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Kissel, John T.
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Mendell, Jerry R.
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Shell, Richard
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PEDIATRIC PULMONOLOGY,
2019, 54 (02)
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Al-Zaidy, Samiah
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Pickard, A. Simon
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Illinois, Dept Pharm Syst Outcomes & Policy, Chicago, IL USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Kotha, Kavitha
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Alfano, Lindsay N.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Lowes, Linda
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Paul, Grace
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Church, Kathleen
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Lehman, Kelly
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Sproule, Douglas M.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Dabbous, Omar
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Maru, Benit
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Berry, Katherine
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Arnold, W. David
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Kissel, John T.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

Mendell, Jerry R.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA
Nationwide Childrens Hosp, Ctr Gene Therapy, Columbus, OH USA
Ohio State Univ, Dept Neurol, Columbus, OH 43210 USA Ohio State Univ, Dept Pediat, Columbus, OH 43210 USA

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机构:
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Al-Zaidy, Samiah
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PEDIATRIC NEUROLOGY,
2014, 51 (05)
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Al-Zaidy, Samiah
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Dept Pediat, Ctr Gene Therapy, Columbus, OH 43205 USA Nationwide Childrens Hosp, Res Inst, Dept Pediat, Ctr Gene Therapy, Columbus, OH 43205 USA

Rodino-Klapac, Louise
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Dept Pediat, Ctr Gene Therapy, Columbus, OH 43205 USA Nationwide Childrens Hosp, Res Inst, Dept Pediat, Ctr Gene Therapy, Columbus, OH 43205 USA

Mendell, Jerry R.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Res Inst, Dept Pediat, Ctr Gene Therapy, Columbus, OH 43205 USA Nationwide Childrens Hosp, Res Inst, Dept Pediat, Ctr Gene Therapy, Columbus, OH 43205 USA
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AVXS-101 (Onasemnogene Abeparvovec) for SMA 1: Comparative Study with a Prospective Natural History Cohort
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Al-Zaidy, Samiah A.
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Kolb, Stephen J.
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Lowes, Linda
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Alfano, Lindsay N.
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Shell, Richard
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Church, Kathleen R.
;
Nagendran, Sukumar
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Sproule, Douglas M.
;
Feltner, Douglas E.
;
Wells, Courtney
;
Ogrinc, Francis
;
Menier, Melissa
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L'Italien, James
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Arnold, W. David
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Kissel, John T.
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Kaspar, Brian K.
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Mendell, Jerry R.
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JOURNAL OF NEUROMUSCULAR DISEASES,
2019, 6 (03)
:307-317

Al-Zaidy, Samiah A.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Wexner Med Ctr, Columbus, OH 43210 USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Kolb, Stephen J.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Neurol, Wexner Med Ctr, Columbus, OH 43210 USA
Ohio State Univ, Dept Biol Chem & Pharmacol, Wexner Med Ctr, Columbus, OH 43210 USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Lowes, Linda
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Wexner Med Ctr, Columbus, OH 43210 USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Alfano, Lindsay N.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Wexner Med Ctr, Columbus, OH 43210 USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Shell, Richard
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Wexner Med Ctr, Columbus, OH 43210 USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Church, Kathleen R.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Nagendran, Sukumar
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Sproule, Douglas M.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Feltner, Douglas E.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Wells, Courtney
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Ogrinc, Francis
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Menier, Melissa
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

L'Italien, James
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Arnold, W. David
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Neurol, Wexner Med Ctr, Columbus, OH 43210 USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Kissel, John T.
论文数: 0 引用数: 0
h-index: 0
机构:
Ohio State Univ, Dept Pediat, Wexner Med Ctr, Columbus, OH 43210 USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Kaspar, Brian K.
论文数: 0 引用数: 0
h-index: 0
机构:
AveXis Inc, Bannockburn, IL USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA

Mendell, Jerry R.
论文数: 0 引用数: 0
h-index: 0
机构:
Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA
Ohio State Univ, Dept Pediat, Wexner Med Ctr, Columbus, OH 43210 USA
Ohio State Univ, Dept Neurol, Wexner Med Ctr, Columbus, OH 43210 USA Nationwide Childrens Hosp, Ctr Gene Therapy Res Inst, Columbus, OH 43205 USA
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Gidaro, Teresa
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D'Amico, Adele
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Dowling, James J.
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2019, 92 (16)
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Annoussamy, Melanie
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Myol, I Mot, Paris, France Inst Myol, I Mot, Paris, France

Lilien, Charlotte
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h-index: 0
机构:
Inst Myol, I Mot, Paris, France Inst Myol, I Mot, Paris, France

Gidaro, Teresa
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Myol, I Mot, Paris, France Inst Myol, I Mot, Paris, France

Gargaun, Elena
论文数: 0 引用数: 0
h-index: 0
机构:
Inst Myol, I Mot, Paris, France Inst Myol, I Mot, Paris, France

Che, Virginie
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h-index: 0
机构:
Inst Myol, I Mot, Paris, France Inst Myol, I Mot, Paris, France

Schara, Ulrike
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Essen Gesamthsch, Paediat Neurol & Neuromuscular Ctr, Essen, Germany Inst Myol, I Mot, Paris, France

Gangfuss, Andrea
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Essen Gesamthsch, Paediat Neurol & Neuromuscular Ctr, Essen, Germany Inst Myol, I Mot, Paris, France

D'Amico, Adele
论文数: 0 引用数: 0
h-index: 0
机构:
Bambino Gesu Childrens Res Hosp IRCCS, Unit Neuromuscular & Neurodegenerat Disorders, Dept Neurosci, Rome, Italy Inst Myol, I Mot, Paris, France

Dowling, James J.
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h-index: 0
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Hosp Sick Children, Div Neurol, Toronto, ON, Canada
Hosp Sick Children, Program Genet & Genome Biol, Toronto, ON, Canada Inst Myol, I Mot, Paris, France

Darras, Basil T.
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h-index: 0
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Boston Childrens Hosp, Boston, MA USA Inst Myol, I Mot, Paris, France

Daron, Aurore
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h-index: 0
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CHR Citadelle, Ctr Reference Neuromusculaire, Liege, Belgium Inst Myol, I Mot, Paris, France

Hernandez, Arturo
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Hosp Puerta Mar, UCI Pediat, Cadiz, Spain Inst Myol, I Mot, Paris, France

de lattre, Capucine
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Hosp Civils Lyon, Hop Croix Rousse, Ctr Reference Malad Neuromusculaires Adulte, Lyon, France Inst Myol, I Mot, Paris, France

Arnal, Jean-Michel
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h-index: 0
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Hop St Musse, Serv Reanimat Polyvalente, Toulon, France Inst Myol, I Mot, Paris, France

Mayer, Michele
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Hop Armand Trousseau, Ctr Reference Malad Neuromusculaires Ile France N, Paris, France Inst Myol, I Mot, Paris, France

Cuisset, Jean-Marie
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h-index: 0
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CHRU, Hop Roger Salengro, Serv Neuropediat, Lille, France Inst Myol, I Mot, Paris, France

Vuillerot, Carole
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h-index: 0
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CHU Lyon, Hop Mere Enfant, Serv Reeduc Pediat Escale, Lyon, France Inst Myol, I Mot, Paris, France

Fontaine, Stephanie
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h-index: 0
机构:
CHU Lyon, Hop Mere Enfant, Serv Reeduc Pediat Escale, Lyon, France Inst Myol, I Mot, Paris, France

Bellance, Remi
论文数: 0 引用数: 0
h-index: 0
机构:
CHU Martinique, Hop Pierre Zobda Quitman, CeRCa, Fort De France, Martinique, France Inst Myol, I Mot, Paris, France

Biancalana, Valerie
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h-index: 0
机构:
Nouvel Hop Civil, Lab Diagnost Genet, Strasbourg, France Inst Myol, I Mot, Paris, France

Buj-Bello, Ana
论文数: 0 引用数: 0
h-index: 0
机构:
Univ Paris Saclay, Univ Evry, INSERM, Genethon,UMR S951, Evry, France Inst Myol, I Mot, Paris, France

Hogrel, Jean-Yves
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h-index: 0
机构:
Inst Myol, Neuromuscular Invest Ctr, Paris, France Inst Myol, I Mot, Paris, France

Landy, Hal
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Valer Therapeut, Concord, MA USA Inst Myol, I Mot, Paris, France

Servais, Laurent
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Aronson, Sem J.
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Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Veron, Philippe
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h-index: 0
机构:
Genethon, 1 Bis Rue Int, F-91000 Evry, France Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Collaud, Fanny
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h-index: 0
机构:
Genethon, 1 Bis Rue Int, F-91000 Evry, France Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

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Hop Antoine Beclere, Dept Hereditary Dis Hepat Metab, Clamart, France Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

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论文数: 0 引用数: 0
h-index: 0
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Genethon, 1 Bis Rue Int, F-91000 Evry, France Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Honnet, Geraldine
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Genethon, 1 Bis Rue Int, F-91000 Evry, France Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

de Knegt, Robert J.
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Erasmus MC, Dept Gastroenterol & Hepatol, Rotterdam, Netherlands Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Junge, Norman
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Hannover Med Sch, Dept Paediat Gastroenterol & Hepatol, Hannover, Germany
Hannover Med Sch, Dept Gastroenterol Hepatol & Endocrinol, Hannover, Germany Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Baumann, Ulrich
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Hannover Med Sch, Dept Paediat Gastroenterol & Hepatol, Hannover, Germany
Hannover Med Sch, Dept Gastroenterol Hepatol & Endocrinol, Hannover, Germany Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Di Giorgio, Angelo
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Papa Giovanni XXIII Hosp, Dept Paediat Hepatol Gastroenterol & Transplantat, Bergamo, Italy Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

D'Antiga, Lorenzo
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Papa Giovanni XXIII Hosp, Dept Paediat Hepatol Gastroenterol & Transplantat, Bergamo, Italy Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Ginocchio, Virginia M.
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机构:
Telethon Inst Genet & Med TIGEM, Pozzuoli, Italy
Federico II Univ Naples, Dept Translat Med, Naples, Italy Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Brunetti-Pierri, Nicola
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Telethon Inst Genet & Med TIGEM, Pozzuoli, Italy
Federico II Univ Naples, Dept Translat Med, Naples, Italy Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Labrune, Philippe
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Hop Antoine Beclere, Dept Hereditary Dis Hepat Metab, Clamart, France Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Beuers, Ulrich
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Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Bosma, Piter J.
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Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands

Mingozzi, Federico
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Genethon, 1 Bis Rue Int, F-91000 Evry, France Univ Amsterdam, Amsterdam UMC, Amsterdam Gastroenterol & Metab, Tytgat Inst Liver & Intestinal Res, Amsterdam, Netherlands