A life-threatening ruxolitinib discontinuation syndrome

被引:40
作者
Coltro, Giacomo [1 ,2 ,3 ]
Mannelli, Francesco [1 ]
Guglielmelli, Paola [1 ,2 ]
Pacilli, Annalisa [1 ,2 ]
Bosi, Alberto [3 ]
Vannucchi, Alessandro Maria [1 ,2 ,3 ]
机构
[1] Azienda Osped Univ Careggi, CRIMM, Florence, Italy
[2] Univ Florence, Dept Expt & Clin Med, DenoThe Excellence Ctr, Florence, Italy
[3] Azienda Osped Univ Careggi, Hematol Unit, Florence, Italy
关键词
POLYCYTHEMIA-VERA; ESSENTIAL THROMBOCYTHEMIA; MYELOID METAPLASIA; MYELOFIBROSIS; PATHOGENESIS; INHIBITOR; NEOPLASMS; THERAPY; JAK2;
D O I
10.1002/ajh.24775
中图分类号
R5 [内科学];
学科分类号
1002 ; 100201 ;
摘要
[No abstract available]
引用
收藏
页码:833 / 838
页数:6
相关论文
共 18 条
[1]   The 2016 revision to the World Health Organization classification of myeloid neoplasms and acute leukemia [J].
Arber, Daniel A. ;
Orazi, Attilio ;
Hasserjian, Robert ;
Thiele, Jurgen ;
Borowitz, Michael J. ;
Le Beau, Michelle M. ;
Bloomfield, Clara D. ;
Cazzola, Mario ;
Vardiman, James W. .
BLOOD, 2016, 127 (20) :2391-2405
[2]   Development and validation of an International Prognostic Score of thrombosis in World Health Organization-essential thrombocythemia (IPSET-thrombosis) [J].
Barbui, Tiziano ;
Finazzi, Guido ;
Carobbio, Alessandra ;
Thiele, Juergen ;
Passamonti, Francesco ;
Rumi, Elisa ;
Ruggeri, Marco ;
Rodeghiero, Francesco ;
Randi, Maria Luigia ;
Bertozzi, Irene ;
Gisslinger, Heinz ;
Buxhofer-Ausch, Veronika ;
De Stefano, Valerio ;
Betti, Silvia ;
Rambaldi, Alessandro ;
Vannucchi, Alessandro M. ;
Tefferi, Ayalew .
BLOOD, 2012, 120 (26) :5128-5133
[3]   Acute respiratory distress syndrome in a patient with primary myelofibrosis after ruxolitinib treatment discontinuation [J].
Beauverd, Yan ;
Samii, Kaveh .
INTERNATIONAL JOURNAL OF HEMATOLOGY, 2014, 100 (05) :498-501
[4]   Ruxolitinib Withdrawal Syndrome Leading to Tumor Lysis [J].
Dai, Tong ;
Friedman, Ellen W. ;
Barta, Stefan K. .
JOURNAL OF CLINICAL ONCOLOGY, 2013, 31 (29) :E430-E432
[5]   JAK Inhibition with Ruxolitinib versus Best Available Therapy for Myelofibrosis [J].
Harrison, Claire ;
Kiladjian, Jean-Jacques ;
Al-Ali, Haifa Kathrin ;
Gisslinger, Heinz ;
Waltzman, Roger ;
Stalbovskaya, Viktoriya ;
McQuitty, Mari ;
Hunter, Deborah S. ;
Levy, Richard ;
Knoops, Laurent ;
Cervantes, Francisco ;
Vannucchi, Alessandro M. ;
Barbui, Tiziano ;
Barosi, Giovanni .
NEW ENGLAND JOURNAL OF MEDICINE, 2012, 366 (09) :787-798
[6]  
Herman Derrick D, 2014, Ann Am Thorac Soc, V11, P1145, DOI 10.1513/AnnalsATS.201403-127CC
[7]   Activating mutation in the tyrosine kinase JAK2 in polycythemia vera, essential thrombocythemia, and myeloid metaplasia with myelofibrosis [J].
Levine, RL ;
Wadleigh, M ;
Cools, J ;
Ebert, BL ;
Wernig, G ;
Huntly, BJP ;
Boggon, TJ ;
Wlodarska, L ;
Clark, JJ ;
Moore, S ;
Adelsperger, J ;
Koo, S ;
Lee, JC ;
Gabriel, S ;
Mercher, T ;
D'Andrea, A ;
Fröhling, S ;
Döhner, K ;
Marynen, P ;
Vandenberghe, P ;
Mesa, RA ;
Tefferi, A ;
Griffin, JD ;
Eck, MJ ;
Sellers, WR ;
Meyerson, M ;
Golub, TR ;
Lee, SJ ;
Gilliland, DG .
CANCER CELL, 2005, 7 (04) :387-397
[8]   Ruxolitinib for the treatment of inadequately controlled polycythaemia vera without splenomegaly (RESPONSE-2): a randomised, open-label, phase 3b study [J].
Passamonti, Francesco ;
Griesshammer, Martin ;
Palandri, Francesca ;
Egyed, Miklos ;
Benevolo, Giulia ;
Devos, Timothy ;
Callum, Jeannie ;
Vannucchi, Alessandro M. ;
Sivgin, Serdar ;
Bensasson, Caroline ;
Khan, Mahmudul ;
Mounedji, Nadjat ;
Saydam, Guray .
LANCET ONCOLOGY, 2017, 18 (01) :88-99
[9]   JAK2V617F complete molecular remission in polycythemia vera/essential thrombocythemia patients treated with ruxolitinib [J].
Pieri, Lisa ;
Pancrazzi, Alessandro ;
Pacilli, Annalisa ;
Rabuzzi, Claudia ;
Rotunno, Giada ;
Fanelli, Tiziana ;
Guglielmelli, Paola ;
Fjerza, Rajmonda ;
Paoli, Chiara ;
Verstovsek, Srdan ;
Vannucchi, Alessandro M. .
BLOOD, 2015, 125 (21) :3352-3353
[10]   Preclinical characterization of the selective JAK1/2 inhibitor INCB018424: therapeutic implications for the treatment of myeloproliferative neoplasms [J].
Quintas-Cardama, Alfonso ;
Vaddi, Kris ;
Liu, Phillip ;
Manshouri, Taghi ;
Li, Jun ;
Scherle, Peggy A. ;
Caulder, Eian ;
Wen, Xiaoming ;
Li, Yanlong ;
Waeltz, Paul ;
Rupar, Mark ;
Burn, Timothy ;
Lo, Yvonne ;
Kelley, Jennifer ;
Covington, Maryanne ;
Shepard, Stacey ;
Rodgers, James D. ;
Haley, Patrick ;
Kantarjian, Hagop ;
Fridman, Jordan S. ;
Verstovsek, Srdan .
BLOOD, 2010, 115 (15) :3109-3117