A Novel AAV-Based Gene Therapy for Spinal Muscular Atrophy

被引：0
作者：
Wu, Zhenhua [1 ]
Zhu, Peixin [1 ]
Wang, Qingzeng [1 ]
Li, Zhongwan [1 ]
Chen, Shuyuan [1 ]
Dai, Li [1 ]
Li, Junhui [1 ]
Wang, Lijun [1 ]
Ye, Guojie [1 ]
机构：
[1] Exegenesis Bio Inc, Spring House, PA USA
来源：
MOLECULAR THERAPY | 2022年 / 30卷 / 04期
关键词：
D O I：
暂无
中图分类号：
Q81 [生物工程学（生物技术）]; Q93 [微生物学];
学科分类号：
071005 ; 0836 ; 090102 ; 100705 ;
摘要：
541
引用
收藏
页码：257 / 257
页数：1
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